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NCT02392637

Gemcitabine Hydrochloride, Cisplatin, and Nab-Paclitaxel in Treating Patients With Advanced or Metastatic Biliary Cancers

Completed Phase 2 Results posted Last updated 2 February 2022
What this trial tests

Phase 2 trial testing Cisplatin in Stage III Intrahepatic Cholangiocarcinoma AJCC v7 in 62 participants. Completed in 13 August 2020.

Timeline
2 April 2015
Primary endpoint
13 August 2020
13 August 2020

Quick facts

Lead sponsorM.D. Anderson Cancer Center
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment62
Start date2 April 2015
Primary completion13 August 2020
Estimated completion13 August 2020
Sites3 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

M.D. Anderson Cancer Center — full company profile →

Who can join

18 and older, any sex, with Stage III Intrahepatic Cholangiocarcinoma AJCC v7 or Stage IIIA Gallbladder Cancer AJCC v7. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Median Progression Free Survival (PFS) Primary · up to 3 years

Progression is defined using Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0), as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions

GroupValue95% CI
High Dosage11.46.0 – 15.6
Low Dosage14.93.8 – NA
Median Overall Survival (OS) Secondary · up to 3 years

The Kaplan-Meier method was used to estimate OS, with surviving patients censored at the time of surgery or at last known follow-up.

GroupValue95% CI
High Dose19.510 – NA
Low Dose15.78.7 – NA
Number of Participants With Treatment Response Rate Secondary · Up to 2 years

Per Response Evaluation Criteria In Solid Tumors Criteria(RECIST v1.1.14) for target lesions and assessed by MRI: Complete Response (CR),Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; Overall Response (OR) = CR + PR.

Disease Control Rate(DCR)
GroupValue95% CI
High Dose25
Low Dose18
Complete Response(CR)
GroupValue95% CI
High Dose0
Low Dose0
Partial Response (PR)
GroupValue95% CI
High Dose14
Low Dose9
Stable Disease(SD)
GroupValue95% CI
High Dose11
Low Dose9
Progressive Disease(PD)
GroupValue95% CI
High Dose3
Low Dose5
Unknown
GroupValue95% CI
High Dose4
Low Dose5

Adverse events — posted to ClinicalTrials.gov

Time frame: up to 3 years. Reporting threshold: 1%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

High Dose
Serious: 5/32 (16%)
Deaths: 1/32
Low Dose
Serious: 1/28 (4%)
Deaths: 0/28

Serious adverse events (2 terms)

ReactionSystemHigh DoseLow Dose
NeutropeniaBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders
Other adverse events (18 terms — click to expand)

ReactionSystemHigh DoseLow Dose
NeutropeniaBlood and lymphatic system disorders
AnemiaBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders
Febrile NeutropeniaBlood and lymphatic system disorders
VomitingGastrointestinal disorders
DiarrheaGastrointestinal disorders
Elevated ALPBlood and lymphatic system disorders
Abdominal InfectionInfections and infestations
ConstipationGastrointestinal disorders
CystitisRenal and urinary disorders
Elevated ASTBlood and lymphatic system disorders
HypokalemiaMetabolism and nutrition disorders
HyponatremiaMetabolism and nutrition disorders
Maculopapular rashSkin and subcutaneous tissue disorders
NauseaGastrointestinal disorders
NeuropathyNervous system disorders
SepsisInfections and infestations
Thromboembolic eventVascular disorders

Most-reported serious reactions: Neutropenia, Thrombocytopenia.

Data from ClinicalTrials.gov NCT02392637 adverse events section.

Sponsor's own description

This phase II trial studies how well gemcitabine hydrochloride, cisplatin, and nab-paclitaxel (paclitaxel albumin-stabilized nanoparticle formulation) work in treating patients with biliary cancers (which includes the gallbladder and bile ducts inside and outside the liver) that have spread to other places in the body and usually cannot be cured or controlled with treatment. Drugs used in chemotherapy, such as gemcitabine hydrochloride, cisplatin, and paclitaxel albumin-stabilized nanoparticle formulation, work in different ways to stop the growth of tumor cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Giving more than one drug (combination chemotherapy) may kill more tumor cells.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Progressing nanotechnology to improve targeted cancer treatment: overcoming hurdles in its clinical implementation.
    Chehelgerdi M, Chehelgerdi M, Allela OQB, Pecho RDC, et al · · 2023 · cited 496× · PMID 37814270 · DOI 10.1186/s12943-023-01865-0
  2. Gemcitabine, Cisplatin, and nab-Paclitaxel for the Treatment of Advanced Biliary Tract Cancers: A Phase 2 Clinical Trial.
    Shroff RT, Javle MM, Xiao L, Kaseb AO, et al · · 2019 · cited 356× · PMID 30998813 · DOI 10.1001/jamaoncol.2019.0270
  3. Biliary tract cancers: current knowledge, clinical candidates and future challenges.
    Tariq NU, McNamara MG, Valle JW. · · 2019 · cited 79× · PMID 31015767 · DOI 10.2147/cmar.s157092
  4. CD8<sup>+</sup> T cell-based cancer immunotherapy.
    Chen Y, Yu D, Qian H, Shi Y, et al · · 2024 · cited 63× · PMID 38685033 · DOI 10.1186/s12967-024-05134-6
  5. Developments in nanotechnology approaches for the treatment of solid tumors.
    Venturini J, Chakraborty A, Baysal MA, Tsimberidou AM. · · 2025 · cited 29× · PMID 40390104 · DOI 10.1186/s40164-025-00656-1
  6. Molecular Subtypes and Precision Oncology in Intrahepatic Cholangiocarcinoma.
    Czauderna C, Kirstein MM, Tews HC, Vogel A, et al · · 2021 · cited 16× · PMID 34202401 · DOI 10.3390/jcm10132803
  7. Advances in platinum-based cancer therapy: overcoming platinum resistance through rational combinatorial strategies.
    Yusoh NA, Ahmad H, Vallis KA, Gill MR. · · 2025 · cited 11× · PMID 40518502 · DOI 10.1007/s12032-025-02812-3
  8. Transarterial chemoembolization plus lenvatinib with or without a PD-1 inhibitor for advanced and metastatic intrahepatic cholangiocarcinoma: a retrospective real-world study.
    Ning Z, Xie L, Yan X, Hua Y, et al · · 2023 · cited 8× · PMID 37660471 · DOI 10.1259/bjr.20230079

Verify or expand the search:

Other trials of Cisplatin

Trials testing the same drug.

Other recruiting trials for Stage III Intrahepatic Cholangiocarcinoma AJCC v7

Currently open trials in the same condition.

Other M.D. Anderson Cancer Center trials

Trials by the same sponsor.

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