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Botulinum Toxin A (Botox )

Assistance Publique - Hôpitaux de Paris · FDA-approved active Small molecule

Botulinum toxin A blocks the release of acetylcholine at the neuromuscular junction by cleaving SNARE proteins, causing temporary muscle paralysis.

Botulinum toxin A blocks the release of acetylcholine at the neuromuscular junction by cleaving SNARE proteins, causing temporary muscle paralysis. Used for Cervical dystonia (spasmodic torticollis), Blepharospasm, Strabismus.

At a glance

Generic nameBotulinum Toxin A (Botox )
SponsorAssistance Publique - Hôpitaux de Paris
Drug classNeurotoxin; acetylcholine release inhibitor
TargetSNARE proteins (specifically SNAP-25); acetylcholine release machinery
ModalitySmall molecule
Therapeutic areaNeurology; Dermatology; Aesthetics
PhaseFDA-approved

Mechanism of action

Botulinum toxin A is a neurotoxin that irreversibly cleaves SNARE (soluble N-ethylmaleimide-sensitive factor attachment receptor) proteins required for acetylcholine vesicle release. This prevents neurotransmitter release at the neuromuscular junction, resulting in flaccid paralysis of targeted muscles. The effect is temporary, lasting 3–4 months, after which nerve terminals regenerate and muscle function returns.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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