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NCT04268303: SERENITY I

Dexmedetomidine in the Treatment of Agitation Associated With Schizophrenia

Completed Phase 3 Results posted Last updated 18 June 2023
What this trial tests

Phase 3 trial testing Sublingual film containing dexmedetomidine (BXCL501) in Agitation in 380 participants. Completed in 6 May 2020.

Timeline
24 January 2020
Primary endpoint
6 May 2020
6 May 2020

Quick facts

Lead sponsorBioXcel Therapeutics Inc
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment380
Start date24 January 2020
Primary completion6 May 2020
Estimated completion6 May 2020
Sites15 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

BioXcel Therapeutics Inc — full company profile →

Who can join

Adults 18 to 75, any sex, with Agitation or Schizophrenia. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Change From Baseline in the Positive and Negative Syndrome Scale- Excited Component (PEC) Total Score Primary · Baseline and 2 hours

The Positive and Negative Syndrome Scale-Excited Component (PEC) includes 5 items-poor impulse control, tension, hostility, uncooperativeness, and excitement-each of which is rated from 1 (minimum) to 7 (maximum); the sum of these 5 items, the PEC total score, ranges from 5 (absence of agitation) to 35 (extremely severe).

Baseline
GroupValue95% CI
120 Micrograms17.5± 2.46
180 Micrograms17.6± 2.69
Placebo17.6± 2.26
2 Hours
GroupValue95% CI
120 Micrograms-8.4± 4.83
180 Micrograms-10.4± 4.34
Placebo-4.7± 4.69
Change From Baseline in the Positive and Negative Syndrome Scale- Excited Component (PEC) Total Score Over Time Secondary · Baseline and 10, 20, 30, 45, 60, 90 minutes post-dose

Effect on agitation onset was measured by change from baseline in the Positive and Negative Syndrome Scale- Excited Component (PEC) total score. The Positive and Negative Syndrome Scale-Excited Component (PEC) includes 5 items-poor impulse control, tension, hostility, uncooperativeness, and excitement-each of which is rated from 1 (minimum) to 7 (maximum); the sum of these 5 items, the PEC total score, ranges from 5 (absence of agitation) to 35 (extremely severe).

Baseline
GroupValue95% CI
120 Micrograms17.5± 2.46
180 Micrograms17.6± 2.69
Placebo17.6± 2.26
10 minutes
GroupValue95% CI
120 Micrograms-1.3± 2.50
180 Micrograms-2.0± 3.19
Placebo-1.3± 2.17
20 minutes
GroupValue95% CI
120 Micrograms-2.8± 4.03
180 Micrograms-3.9± 4.54
Placebo-2.5± 3.20
30 minutes
GroupValue95% CI
120 Micrograms-4.4± 4.90
180 Micrograms-5.7± 5.27
Placebo-3.1± 3.56
45 minutes
GroupValue95% CI
120 Micrograms-5.7± 5.18
180 Micrograms-7.6± 5.32
Placebo-3.6± 3.78
60 minutes
GroupValue95% CI
120 Micrograms-6.9± 5.06
180 Micrograms-8.8± 4.96
Placebo-4.1± 4.16
90 minutes
GroupValue95% CI
120 Micrograms-8.0± 5.00
180 Micrograms-9.8± 4.60
Placebo-4.6± 4.38

Adverse events — posted to ClinicalTrials.gov

Time frame: 30 days. Reporting threshold: 3%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

120 Micrograms
Serious: 0/129 (0%)
Deaths: 0/129
180 Micrograms
Serious: 0/126 (0%)
Deaths: 0/126
Placebo
Serious: 0/126 (0%)
Deaths: 0/126
Other adverse events (8 terms — click to expand)

ReactionSystem120 Micrograms180 MicrogramsPlacebo
SomnolenceNervous system disorders
Dry mouthGastrointestinal disorders
DizzinessNervous system disorders
HypotensionVascular disorders
Hypoesthesia oralNervous system disorders
Orthostatic hypotensionVascular disorders
HeadacheNervous system disorders
Paresthesia oralNervous system disorders

Data from ClinicalTrials.gov NCT04268303 adverse events section.

Sponsor's own description

This is a definitive study to support the safety and efficacy evaluation of BXCL501 for the acute treatment of agitation in schizophrenia. The BXCL501-301 study is designed to characterize the efficacy, safety and tolerability of BXCL501 (sublingual film formulation of DEX, HCl) in agitation associated with schizophrenia, schizoaffective disorder or schizophreniform disorder.

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Sublingual Dexmedetomidine for the Treatment of Acute Agitation in Adults With Schizophrenia or Schizoaffective Disorder: A Randomized Placebo-Controlled Trial.
    Citrome L, Preskorn SH, Lauriello J, Krystal JH, et al · · 2022 · cited 17× · PMID 36198061 · DOI 10.4088/jcp.22m14447
  2. Sublingual Dexmedetomidine for Agitation Associated with Schizophrenia or Bipolar Disorder: A Post Hoc Analysis of Number Needed to Treat, Number Needed to Harm, and Likelihood to be Helped or Harmed.
    Citrome L, Risinger R, Rajachandran L, Robison H. · · 2022 · cited 7× · PMID 36002761 · DOI 10.1007/s12325-022-02274-3
  3. Risk assessment for aggressive behaviour in schizophrenia.
    Välimäki M, Lantta T, Kontio R. · · 2024 · cited 4× · PMID 38695777 · DOI 10.1002/14651858.cd012397.pub2

Verify or expand the search:

Other trials of Sublingual film containing dexmedetomidine (BXCL501)

Trials testing the same drug.

Other recruiting trials for Agitation

Currently open trials in the same condition.

Other BioXcel Therapeutics Inc trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04268303.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing