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NCT04179461

Personalized Treatment Algorithms for Difficult-to-treat Asthma

Completed Phase 2 Results posted Last updated 20 August 2021
What this trial tests

Phase 2 trial testing Cholecalciferol in Asthma in Children in 21 participants. Completed in 3 October 2019.

Timeline
16 March 2018
Primary endpoint
3 October 2019
3 October 2019

Quick facts

Lead sponsorChildren's Hospital Medical Center, Cincinnati
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment21
Start date16 March 2018
Primary completion3 October 2019
Estimated completion3 October 2019
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Children's Hospital Medical Center, Cincinnati

Who can join

Adults 6 to 17, any sex, with Asthma in Children. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Change in Composite Asthma Severity Index (CASI) Primary · Baseline to 12 months

CASI was measured by questionnaire and is a severity score of symptom burden, exacerbations, healthcare utilization, lung function and dose of inhaled corticosteroids. The change in CASI score was calculated between V1 (Baseline), V2 (Guideline Care - before intervention), and V3 (12 Months). \[The CASI score has a minimum value = 0, maximum value = 20, a higher score indicates greater asthma severity\]

V1
GroupValue95% CI
Personalized Treatment55 – 6
V2
GroupValue95% CI
Personalized Treatment55 – 5
V3
GroupValue95% CI
Personalized Treatment55 – 5
Asthma Control Test (ACT) Secondary · Baseline to 12 months

ACT was measured by questionnaire, assessing frequency of reported asthma symptoms, rescue medication use, the effect of asthma on daily functioning, and overall asthma control. The change in ACT score was calculated between V1 (Baseline), V2 (Guideline Care - before intervention), and V3 (12 Months). \[The ACT score has a minimum value = 5, maximum value = 25, a score 19 indicates well-controlled asthma\]

V1
GroupValue95% CI
Personalized Treatment23.020.0 – 23.0
V2
GroupValue95% CI
Personalized Treatment21.718.2 – 24.2
V3
GroupValue95% CI
Personalized Treatment22.518.2 – 24.2
Pulmonary Function Measured by Spirometry: Forced Expiratory Volume in 1 Second (FEV1) / Forced Vital Capacity (FVC) Secondary · Baseline to 12 months

FEV1 is air volume exhaled in 1 second during spirometry. Forced vital capacity is the amount of air that can be forcibly exhaled from the lungs after taking the deepest breath possible. The change in FEV1/FVC was calculated between V1 (Baseline), V2 (Guideline Care - before intervention), and V3 (12 Months). This will be used as a measurement in asthma severity. \[A lower FEV1/FVC ratio indicates more severe asthma\]

V1
GroupValue95% CI
Personalized Treatment0.810.76 – 0.86
V2
GroupValue95% CI
Personalized Treatment0.80.76 – 0.85
V3
GroupValue95% CI
Personalized Treatment0.80.77 – 0.87
Adherence of Asthma Controller Medication Secondary · Baseline to 12 months

Adherence was measured using the Propeller Health Inhaler monitor and web-based software management platform that tracks adherence of asthma medications. The change in adherence was calculated between V1 (baseline) to V3 (12 Months).

V1
GroupValue95% CI
Personalized Treatment4221 – 57
V3
GroupValue95% CI
Personalized Treatment3614 – 53

Adverse events — posted to ClinicalTrials.gov

Time frame: 1 year. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Personalized Treatment
Serious: 1/21 (5%)
Deaths: 0/21

Serious adverse events (2 terms)

ReactionSystemPersonalized Treatment
Major Depressive DisorderPsychiatric disorders
Psychiatric EvaluationPsychiatric disorders
Other adverse events (6 terms — click to expand)

ReactionSystemPersonalized Treatment
Asthma ExacerbationRespiratory, thoracic and mediastinal disorders
Streptococcal PharyngitisInfections and infestations
Ankle InjuryMusculoskeletal and connective tissue disorders
InfluenzaInfections and infestations
Viral GastroenteritisInfections and infestations
SinusitisInfections and infestations

Most-reported serious reactions: Major Depressive Disorder, Psychiatric Evaluation.

Data from ClinicalTrials.gov NCT04179461 adverse events section.

Sponsor's own description

Asthma is a common, complex and costly chronic condition. Moreover, asthma is heterogeneous in terms of treatment response. This heterogeneity contributes to the difficulty in both studying and treating asthma. This is a pilot study to improve health outcomes in youths with difficult to treat asthma with ongoing symptoms and healthcare utilization despite medium to high doses of inhaled corticosteroids. Asthma heterogeneity in both disease pathophysiology and treatment response contributes to the difficulty in both studying and managing asthma. In order to begin to develop personalized algorithms for patients, investigators need to model novel biomarkers and other factors that contribute to individual differences in asthma outcome and test other factors that contribute to individual differences in asthma outcome and test personalized treatment strategies.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Treatment by biomarker-informed endotype vs guideline care in children with difficult-to-treat asthma.
    Guilbert TW, Biagini JM, Ramsey RR, Keidel K, et al · · 2022 · cited 2× · PMID 35123074 · DOI 10.1016/j.anai.2022.01.030

Verify or expand the search:

Other trials of Cholecalciferol

Trials testing the same drug.

Other recruiting trials for Asthma in Children

Currently open trials in the same condition.

Other Children's Hospital Medical Center, Cincinnati trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04179461.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing