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ISIS-PTP1BRx

Ionis Pharmaceuticals, Inc. · Phase 2 active Small molecule

ISIS-PTP1BRx is a Antisense oligonucleotide (PTP1B inhibitor) Small molecule drug developed by Ionis Pharmaceuticals, Inc.. It is currently in Phase 2 development for Type 2 diabetes mellitus, Obesity.

ISIS-PTP1BRx is an antisense oligonucleotide that inhibits protein tyrosine phosphatase 1B (PTP1B) to improve insulin signaling and glucose metabolism.

ISIS-PTP1BRx is an antisense oligonucleotide that inhibits protein tyrosine phosphatase 1B (PTP1B) to improve insulin signaling and glucose metabolism. Used for Type 2 diabetes mellitus, Obesity.

Likelihood of approval
15.3% vs 15.3% industry baseline
If approved by FDA: likely 2031–2034
Steps remaining: Phase 3 → NDA/BLA submission
Confidence: Medium
Why this estimate
  • Baseline phase 2 → approval rate +15.3pp
    Industry-wide phase 2 drugs reach approval ~15.3% of the time (BIO/Informa 2023 industry benchmark across all therapeutic areas).
Predicted approval windows by jurisdiction (conditional on FDA approval)
Regulator Country Likely year Lag vs FDA
FDA US 2031–2034
EMA EU 2032–2035 +0.7 yr
MHRA GB 2032–2035 +0.7 yr
Health Canada CA 2032–2036 +0.9 yr
TGA AU 2032–2036 +1.2 yr
PMDA JP 2032–2036 +1.5 yr
NMPA CN 2033–2037 +2.3 yr
MFDS KR 2032–2036 +1.4 yr
CDSCO IN 2032–2037 +1.8 yr
ANVISA BR 2033–2037 +2.3 yr

Hover any row for the lag rationale. Lag estimates are reduced when the drug has FDA Breakthrough or EMA PRIME designation (sponsors file globally in parallel).

Estimate based on the BIO/Informa industry phase transition rates plus per-drug modifiers for therapeutic area, sponsor type, FDA designations, mechanism, and trial design. Per-jurisdiction lags from Tufts CSDD international approval studies. Not investment, clinical or regulatory advice. Methodology: /methodology#likelihood.

At a glance

Generic nameISIS-PTP1BRx
SponsorIonis Pharmaceuticals, Inc.
Drug classAntisense oligonucleotide (PTP1B inhibitor)
TargetPTP1B (Protein Tyrosine Phosphatase 1B)
ModalitySmall molecule
Therapeutic areaMetabolic/Endocrinology
PhasePhase 2

Mechanism of action

PTP1B is a negative regulator of insulin receptor signaling; by reducing PTP1B expression, the drug enhances insulin sensitivity and glucose uptake in target tissues. This mechanism is intended to improve glycemic control and metabolic parameters in metabolic diseases. The antisense approach allows selective reduction of the target protein without affecting other pathways.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:

Frequently asked questions about ISIS-PTP1BRx

What is ISIS-PTP1BRx?

ISIS-PTP1BRx is a Antisense oligonucleotide (PTP1B inhibitor) drug developed by Ionis Pharmaceuticals, Inc., indicated for Type 2 diabetes mellitus, Obesity.

How does ISIS-PTP1BRx work?

ISIS-PTP1BRx is an antisense oligonucleotide that inhibits protein tyrosine phosphatase 1B (PTP1B) to improve insulin signaling and glucose metabolism.

What is ISIS-PTP1BRx used for?

ISIS-PTP1BRx is indicated for Type 2 diabetes mellitus, Obesity.

Who makes ISIS-PTP1BRx?

ISIS-PTP1BRx is developed by Ionis Pharmaceuticals, Inc. (see full Ionis Pharmaceuticals, Inc. pipeline at /company/ionis-pharmaceuticals-inc).

What drug class is ISIS-PTP1BRx in?

ISIS-PTP1BRx belongs to the Antisense oligonucleotide (PTP1B inhibitor) class. See all Antisense oligonucleotide (PTP1B inhibitor) drugs at /class/antisense-oligonucleotide-ptp1b-inhibitor.

What development phase is ISIS-PTP1BRx in?

ISIS-PTP1BRx is in Phase 2.

What are the side effects of ISIS-PTP1BRx?

Common side effects of ISIS-PTP1BRx include Injection site reactions, Liver enzyme elevation, Platelet reduction.

What does ISIS-PTP1BRx target?

ISIS-PTP1BRx targets PTP1B (Protein Tyrosine Phosphatase 1B) and is a Antisense oligonucleotide (PTP1B inhibitor).

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing