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Eptacog alfa (NovoSeven)

Novo Nordisk A/S · FDA-approved active Small molecule

Eptacog alfa is a recombinant Factor VIIa that bypasses upstream coagulation defects by directly activating Factor X on the tissue factor pathway to initiate thrombin generation and hemostasis.

Eptacog alfa is a recombinant Factor VIIa that bypasses upstream coagulation defects by directly activating Factor X on the tissue factor pathway to initiate thrombin generation and hemostasis. Used for Hemophilia A with inhibitors, Hemophilia B with inhibitors, Factor VII deficiency.

At a glance

Generic nameEptacog alfa (NovoSeven)
SponsorNovo Nordisk A/S
Drug classRecombinant coagulation factor
TargetTissue factor (TF) / Factor X
ModalitySmall molecule
Therapeutic areaHematology
PhaseFDA-approved

Mechanism of action

Eptacog alfa (recombinant human Factor VIIa) binds to tissue factor on cell surfaces and directly activates Factor X to Factor Xa, bypassing the need for upstream factors VIII and IX. This allows patients with deficiencies or inhibitors in the intrinsic pathway to generate thrombin and form stable clots. It is particularly useful in hemophilia A and B patients with inhibitors who cannot use conventional factor replacement therapy.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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