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CSL300

CSL Behring · Phase 2 active Small molecule

CSL300 is a recombinant human monoclonal antibody that targets the complement system.

CSL300 is a recombinant human monoclonal antibody that targets the complement system. Used for Paroxysmal nocturnal hemoglobinuria (PNH).

At a glance

Generic nameCSL300
Also known asClazakizumab
SponsorCSL Behring
Drug classComplement inhibitor
TargetC5
ModalitySmall molecule
Therapeutic areaImmunology
PhasePhase 2

Mechanism of action

CSL300 works by inhibiting the complement system, specifically the C5 component, to prevent excessive inflammation and tissue damage. This mechanism is thought to be beneficial in treating conditions associated with complement system dysregulation.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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