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allo-APZ2-OTS

RHEACELL GmbH & Co. KG · Phase 3 active Small molecule Under review

allo-APZ2-OTS is a S1P receptor modulator Small molecule drug developed by RHEACELL GmbH & Co. KG. It is currently in Phase 3 development for Multiple sclerosis.

Allo-APZ2-OTS is a small molecule that targets the sphingosine-1-phosphate receptor 1 (S1PR1).

Allo-APZ2-OTS is a small molecule being studied in a Phase III clinical trial for the treatment of Epidermolysis Bullosa. The trial is a double-blind, randomized, placebo-controlled study that involves the administration of allo-APZ2-OTS to patients with Epidermolysis Bullosa.

Likelihood of approval
59.3% vs 58.3% industry baseline
If approved by FDA: likely 2028–2030
Steps remaining: NDA/BLA submission
Confidence: High
Why this estimate
  • Baseline phase 3 → approval rate +58.3pp
    Industry-wide phase 3 drugs reach approval ~58.3% of the time (BIO/Informa 2023 industry benchmark across all therapeutic areas).
  • Immunology slight uplift +1.0pp
    Mature endpoint landscape (ACR, DAS28, PASI) makes immunology approvals slightly more predictable.
Predicted approval windows by jurisdiction (conditional on FDA approval)
Regulator Country Likely year Lag vs FDA
FDA US 2028–2030
EMA EU 2029–2031 +0.7 yr
MHRA GB 2029–2031 +0.7 yr
Health Canada CA 2029–2032 +0.9 yr
TGA AU 2029–2032 +1.2 yr
PMDA JP 2029–2032 +1.5 yr
NMPA CN 2030–2033 +2.3 yr
MFDS KR 2029–2032 +1.4 yr
CDSCO IN 2029–2033 +1.8 yr
ANVISA BR 2030–2033 +2.3 yr

Hover any row for the lag rationale. Lag estimates are reduced when the drug has FDA Breakthrough or EMA PRIME designation (sponsors file globally in parallel).

Estimate based on the BIO/Informa industry phase transition rates plus per-drug modifiers for therapeutic area, sponsor type, FDA designations, mechanism, and trial design. Per-jurisdiction lags from Tufts CSDD international approval studies. Not investment, clinical or regulatory advice. Methodology: /methodology#likelihood.

At a glance

Generic nameallo-APZ2-OTS
SponsorRHEACELL GmbH & Co. KG
Drug classS1P receptor modulator
TargetS1PR1
ModalitySmall molecule
Therapeutic areaAutoimmune diseases
PhasePhase 3

Mechanism of action

By binding to S1PR1, allo-APZ2-OTS modulates the immune response and has shown potential in treating autoimmune diseases. The exact mechanism of action is still being researched, but it is believed to involve the regulation of immune cell trafficking and function.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:

Frequently asked questions about allo-APZ2-OTS

What is allo-APZ2-OTS?

allo-APZ2-OTS is a S1P receptor modulator drug developed by RHEACELL GmbH & Co. KG, indicated for Multiple sclerosis.

How does allo-APZ2-OTS work?

Allo-APZ2-OTS is a small molecule that targets the sphingosine-1-phosphate receptor 1 (S1PR1).

What is allo-APZ2-OTS used for?

allo-APZ2-OTS is indicated for Multiple sclerosis.

Who makes allo-APZ2-OTS?

allo-APZ2-OTS is developed by RHEACELL GmbH & Co. KG (see full RHEACELL GmbH & Co. KG pipeline at /company/rheacell-gmbh-co-kg).

What drug class is allo-APZ2-OTS in?

allo-APZ2-OTS belongs to the S1P receptor modulator class. See all S1P receptor modulator drugs at /class/s1p-receptor-modulator.

What development phase is allo-APZ2-OTS in?

allo-APZ2-OTS is in Phase 3.

What are the side effects of allo-APZ2-OTS?

Common side effects of allo-APZ2-OTS include Headache, Nausea, Diarrhea.

What does allo-APZ2-OTS target?

allo-APZ2-OTS targets S1PR1 and is a S1P receptor modulator.

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing