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Cobalamin deficiency — Treatment Landscape & Competitive Intelligence
5 marketed
0 Phase 3
0 Phase 2
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Marketed treatment landscape
| Drug | Generic | Sponsor | Class | Target | Line of therapy | First approval |
|---|---|---|---|---|---|---|
| Thiamine Hydrochloride | THIAMINE | Pfizer | thiamine (vit B1) | Heat shock protein HSP 90-alpha | 1993-01-01 | |
| Cyanokit | HYDROXOCOBALAMIN | Btg Intl | Antidote | 1978-01-01 | ||
| Cyanocobalamin Co 57 | cyanocobalamin (57Co) | Mallinckrodt | Radioactive Diagnostic Agent | Cob(I)yrinic acid a,c-diamide adenosyltransferase, mitochondrial, Methionine synthase, Methionine synthase reductase | 1968-01-01 | |
| Hydroxycobalamin | Hydroxycobalamin | Christian Medical College, Vellore, India | ||||
| Thiamin | Thiamin | Hospital Sao Domingos | Thiamin pyrophosphokinase 1, Thiamine transporter 1, Thiamine-triphosphatase |
Phase 3 pipeline
Phase 2 pipeline
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Sponsor landscape
- · 4 drugs in Cobalamin deficiency
- Btg Intl · 1 drug in Cobalamin deficiency
- Christian Medical College, Vellore, India · 1 drug in Cobalamin deficiency
- Hospital Sao Domingos · 1 drug in Cobalamin deficiency
- Mallinckrodt · 1 drug in Cobalamin deficiency
- Pfizer · 1 drug in Cobalamin deficiency
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Cite this brief
Drug Landscape (2026). Cobalamin deficiency — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/cobalamin-deficiency. Accessed 2026-06-10.
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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing