What's in Ultragenyx Pharmaceutical Inc's pipeline?

Ultragenyx Pharmaceutical Inc has 10 drugs in our index: 1 marketed, 0 filed, 4 in Phase 3, 3 in Phase 2, 2 in Phase 1.

Which companies overlap with Ultragenyx Pharmaceutical Inc's portfolio?

Top competitors by shared drug class: Alexion Pharmaceuticals, Inc., Amgen, Arbeitsgemeinschaft medikamentoese Tumortherapie, Assistance Publique - Hôpitaux de Paris, Avidity Biosciences, Inc..

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Subscribe to /feed/company/ultragenyx-pharmaceutical-inc.xml in any RSS reader. Every regulatory action and pipeline update lands in your feed.

Last reviewed 2026-05-18 · How we verify

Ultragenyx Pharmaceutical Inc — Portfolio Competitive Intelligence Brief

Name: Drug Landscape Pharmaceutical Database
Creator: Drug Landscape
Published: 2026-01-01
License: https://creativecommons.org/licenses/by/4.0/

Ultragenyx Pharmaceutical Inc pipeline: 1 marketed, 0 filed, 4 Phase 3, 3 Phase 2. Recent regulatory actions, upcoming PDUFA, patent timeline, top competitor overlap.

1 marketed 0 filed 4 Phase 3 3 Phase 2 2 Phase 1 Live · 30-min refresh

Portfolio leaders (marketed + Phase 3 / filed)

Drug	Generic	Phase	Class	Target	Area
Mepsevii	Mepsevii	marketed			Other
Placebo for oral corticosteroids	Placebo for oral corticosteroids	phase 3
GTX-102	GTX-102	phase 3	Antisense oligonucleotide	FUS mRNA	Neurology
Antipyretic	Antipyretic	phase 3			Other
UX003	UX003	phase 3	Monoclonal antibody	ANGPTL3	Cardiovascular

Therapeutic area mix

Other · 2
Cardiovascular · 1
Neurology · 1

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this portfolio.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this portfolio.

Patent timeline (forward window)

No upcoming patent expiries for this portfolio.

Competitive overlap (companies sharing drug classes)

Alexion Pharmaceuticals, Inc. · 1 shared drug class
Amgen · 1 shared drug class
Arbeitsgemeinschaft medikamentoese Tumortherapie · 1 shared drug class
Assistance Publique - Hôpitaux de Paris · 1 shared drug class
Avidity Biosciences, Inc. · 1 shared drug class
Azienda Ospedaliera Universitaria Integrata Verona · 1 shared drug class
Baxalta now part of Shire · 1 shared drug class
AgeneBio · 1 shared drug class

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Cite this brief

Drug Landscape (2026). Ultragenyx Pharmaceutical Inc — Portfolio Competitive Intelligence Brief. https://druglandscape.com/ci/company/ultragenyx-pharmaceutical-inc. Accessed 2026-05-18.