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BioMarin Pharmaceutical Inc. — Portfolio Competitive Intelligence Brief

BioMarin Pharmaceutical Inc. (BMRN) pipeline: 6 marketed, 0 filed, 0 Phase 3, 0 Phase 2. Recent regulatory actions, upcoming PDUFA, patent timeline, top competitor overlap.

BMRN (NASDAQ) 6 marketed 0 filed 0 Phase 3 0 Phase 2 0 Phase 1 Live · 30-min refresh

Portfolio leaders (marketed + Phase 3 / filed)

DrugGenericPhaseClassTargetAreaFirst approval
Roctavian VALOCTOCOGENE ROXAPARVOVEC marketed Rare Disease 2022-01-01
Rhttp1 CERLIPONASE ALFA marketed Hydrolytic Lysosomal N-terminal Tripeptidyl Peptidase Neuroscience 2017-01-01
Rhgalns ELOSULFASE ALFA marketed Hydrolytic Lysosomal Glycosaminoglycan-specific Enzyme [EPC] N-acetylgalactosamine-6-sulfatase Metabolic 2014-01-01
Kuvan SAPROPTERIN marketed Phenylalanine Hydroxylase Activator Nitric oxide synthase, brain Oncology 2007-01-01
Aryplase GALSULFASE marketed Hydrolytic Lysosomal Glycosaminoglycan-specific Enzyme [EPC] Metabolic 2005-01-01
Aldurazyme LARONIDASE marketed Hydrolytic Lysosomal Glycosaminoglycan-specific Enzyme [EPC] Metabolic 2003-01-01

Therapeutic area mix

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this portfolio.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this portfolio.

Patent timeline (forward window)

No upcoming patent expiries for this portfolio.

Competitive overlap (companies sharing drug classes)

  1. Takeda · 1 shared drug class

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Cite this brief

Drug Landscape (2026). BioMarin Pharmaceutical Inc. — Portfolio Competitive Intelligence Brief. https://druglandscape.com/ci/company/biomarin. Accessed 2026-05-13.

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