BioMarin Pharmaceutical Inc. (BMRN)
Quick facts
| Ticker | BMRN (NASDAQ) |
|---|
Marketed products
- Rhgalns · Metabolic · revenue 500
VIMIZIM provides exogenous N-acetylgalactosamine-6-sulfatase to increase the catabolism of GAGs KS and C6S in lysosomes. - Aryplase · Metabolic · revenue 400
Aryplase breaks down accumulated glycosaminoglycans in lysosomes to treat Maroteaux-Lamy syndrome. - Aldurazyme · Metabolic · revenue 300
Aldurazyme breaks down abnormal sugar molecules in the body to treat Mucopolysaccharidosis I. - Kuvan · Oncology · revenue 300
Kuvan works by activating the enzyme Phenylalanine Hydroxylase to break down phenylalanine. - Rhttp1 · Neuroscience
Cerliponase alfa works by inhibiting the breakdown of a protein called tripeptidyl peptidase, which is deficient in patients with late-infantile neuronal ceroid lipofuscinosis. - Roctavian · Rare Disease
Roctavian introduces a functional copy of the F8 gene into cells to produce factor VIII protein.
Competitive intelligence
For the full portfolio CI brief — phase mix, recent regulatory actions, upcoming PDUFA dates, patent timeline, class-overlap with competitors: