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ARINA-1 — Competitive Intelligence Brief
phase 3
CFTR corrector
CFTR
Respiratory
Small molecule
Live · refreshed every 30 min
Target snapshot
ARINA-1 (ARINA-1) — Renovion, Inc.. ARINA-1 is a small molecule inhaled cystic fibrosis transmembrane conductance regulator (CFTR) corrector.
Comparator set (6 drugs)
| Drug | Generic | Sponsor | Phase | Class | Target | Approval / PDUFA |
|---|---|---|---|---|---|---|
| ARINA-1 TARGET | ARINA-1 | Renovion, Inc. | phase 3 | CFTR corrector | CFTR | |
| Symdeko (Copackaged) | TEZACAFTOR | Vertex Pharms | marketed | CFTR | 2018-01-01 | |
| IVA | IVA | Vertex Pharmaceuticals Incorporated | marketed | CFTR potentiator | CFTR (cystic fibrosis transmembrane conductance regulator) | |
| Ivacaftor+lumacaftor | Ivacaftor+lumacaftor | Assistance Publique - Hôpitaux de Paris | marketed | CFTR modulator combination (corrector + potentiator) | CFTR (cystic fibrosis transmembrane conductance regulator) | |
| Ivacaftor and Symdeko | Ivacaftor and Symdeko | University of Alabama at Birmingham | marketed | CFTR modulator (potentiator and corrector combination) | CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) | |
| TEZ | TEZ | Vertex Pharmaceuticals Incorporated | marketed | CFTR corrector | CFTR (cystic fibrosis transmembrane conductance regulator) | |
| Ivacaftor/Ataluren | Ivacaftor/Ataluren | University of Alabama at Birmingham | marketed | CFTR modulator combination | CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) |
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Patent timeline (forward window)
- — Symdeko (Copackaged) · 8354427 · US
- — Symdeko (Copackaged) · 9931334 · US
- — Symdeko (Copackaged) · 9670163 · US
- — Symdeko (Copackaged) · 8754224 · US
- — Symdeko (Copackaged) · 8410274 · US
- — Symdeko (Copackaged) · 10239867 · US
- — Symdeko (Copackaged) · 9974781 · US
- — Symdeko (Copackaged) · 11639347 · US
- — Symdeko (Copackaged) · 10022352 · US
- — Symdeko (Copackaged) · 8598181 · US
- — Symdeko (Copackaged) · 7645789 · US
- — Symdeko (Copackaged) · 8623905 · US
- — Symdeko (Copackaged) · 7495103 · US
- — Symdeko (Copackaged) · 7776905 · US
- — Symdeko (Copackaged) · 8324242 · US
- — Symdeko (Copackaged) · 8415387 · US
- — Symdeko (Copackaged) · 11564916 · US
- — Symdeko (Copackaged) · 10646481 · US
- — Symdeko (Copackaged) · 10081621 · US
- — Symdeko (Copackaged) · 11578062 · US
- — Symdeko (Copackaged) · 10058546 · US
- — Symdeko (Copackaged) · 9012496 · US
- — Symdeko (Copackaged) · 10206877 · US
Sponsor landscape (CFTR corrector class)
- Vertex Pharmaceuticals Incorporated · 3 drugs in this class
- Chiesi Farmaceutici S.p.A. · 1 drug in this class
- Renovion, Inc. · 1 drug in this class
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Cite this brief
Drug Landscape (2026). ARINA-1 — Competitive Intelligence Brief. https://druglandscape.com/ci/arina-1. Accessed 2026-05-14.
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