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NCT06360289

Observational Study of Neurofilament Light Chain (NfL) as a Biomarker in Asymptomatic Carriers of the Transthyretin (TTR) Variants and Patients With Hereditary Transthyretin-mediated (hATTR) Amyloidosis With Polyneuropathy

Recruiting now Last updated 24 December 2025
What this trial tests

trial testing Standard of Care in Hereditary Amyloidosis, Transthyretin-Related in 500 participants. Currently enrolling.

Timeline
25 April 2024
Primary endpoint
1 December 2027
1 December 2027

Quick facts

Lead sponsorAlnylam Pharmaceuticals
StatusRecruiting now
Study typeOBSERVATIONAL
Enrollment500
Start date25 April 2024
Primary completion1 December 2027
Estimated completion1 December 2027
Sites1 location across France

Drugs / interventions tested

Conditions studied

Sponsor

Alnylam Pharmaceuticals — full company profile →

Who can join

Eligibility, any sex, with Hereditary Amyloidosis, Transthyretin-Related or Asymptomatic Carrier State. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This is a single-center observational study evaluating the potential value of NfL as a biomarker for diagnosis, detection of disease onset, monitoring of disease progression, and treatment response in asymptomatic carriers of TTR variants and symptomatic hATTR amyloidosis patients with polyneuropathy.

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other trials of Standard of Care

Trials testing the same drug.

Other recruiting trials for Hereditary Amyloidosis, Transthyretin-Related

Currently open trials in the same condition.

Other Alnylam Pharmaceuticals trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing