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NCT07080268
Validation of a Questionnaire for Quality of Life Assessment in Patients With Transthyretin Amyloidosis.
trial in Amyloidosis in Transthyretin (TTR) in 70 participants. Participants enrolled and being followed up; not accepting new ones.
1 September 2025
Quick facts
| Lead sponsor | Hospital General de Niños Pedro de Elizalde |
|---|---|
| Status | Active, enrolled |
| Study type | OBSERVATIONAL |
| Enrollment | 70 |
| Start date | 20 June 2025 |
| Primary completion | 1 September 2025 |
| Estimated completion | 30 December 2025 |
| Sites | 1 location across Argentina |
Conditions studied
- Amyloidosis in Transthyretin (TTR) — all drugs for Amyloidosis in Transthyretin (TTR) →
- Hereditary Amyloidosis, Transthyretin-Related — all drugs for Hereditary Amyloidosis, Transthyretin-Related →
Sponsor
Hospital General de Niños Pedro de Elizalde
Who can join
18 and older, any sex, with Amyloidosis in Transthyretin (TTR) or Hereditary Amyloidosis, Transthyretin-Related. Patients with the condition only — healthy volunteers not accepted.
Sponsor's own description
Prospective study of development and validation of a questionnaire on quality of life in patients with Hereditary Amyloidosis The questionnaire development process will include 4 medical specialists experts in Transthyretin Amyloidosis (2 neurologists, 1 cardiologist, 1 physician clinical/hepathologist), 1 psychologist; 1 social worker; and 3 patients (with confirmed Hereditary amyloidosis) members of ALAPA. (Local PAG) Population and sample:
Publications & conference data
No peer-reviewed publications indexed yet for this trial.
Verify or expand the search:
- PubMed search for NCT07080268
- Europe PMC full search
- ASCO Meeting Library
- ESMO Meeting Library
- bioRxiv preprints
- medRxiv preprints
- Google Scholar
Related trials
Other recruiting trials for Amyloidosis in Transthyretin (TTR)
Currently open trials in the same condition.
- NCT07213297 — Comprehensive Program for Hereditary Transthyretin Amyloidosis · recruiting
Other Hospital General de Niños Pedro de Elizalde trials
Trials by the same sponsor.
- NCT07202585 — Analysis of Variability in the Management of Respiratory Infections in Hospitalized Patients Under 2 Years of Age · completed
- NCT05402397 — Losartan and Uric Acid Metabolism in Children With Proteinuric Nephropathies · Phase 4 · completed
- NCT04736680 — Pediatric Virtual Visits as a Strategy for Access to Care During the COVID-19 Pandemic in a Pediatric Hospital · completed
- NCT03776851 — Erythropoietin in Hemolytic Uremic Syndrome · Phase 4 · completed
- NCT06077630 — Non-attendance Prediction Models to Pediatric Outpatient Appointments · completed
Verify against primary sources
- ClinicalTrials.gov — authoritative US registry record
- WHO ICTRP — international registry index
- EU Clinical Trials Register
- Sponsor press releases (Google)
- Trial protocol + status: ClinicalTrials.gov NCT07080268 (US National Library of Medicine, public domain)
- Drug + disease cross-links: matched in real time against Drug Landscape's normalised drug + company + condition tables
- Sponsor: as reported to ClinicalTrials.gov by Hospital General de Niños Pedro de Elizalde
- Last refreshed: 23 July 2025
Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT07080268.
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing