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NCT06106022

A Study to Evaluate Vonoprazan in Children Who Have Symptomatic Gastroesophageal Reflux Disease

Completed Phase 1 Results posted Last updated 19 December 2024
What this trial tests

Phase 1 trial testing Vonoprazan in Gastroesophageal Reflux Disease in 22 participants. Completed in 29 April 2024.

Timeline
1 November 2023
Primary endpoint
16 April 2024
29 April 2024

Quick facts

Lead sponsorPhathom Pharmaceuticals, Inc.
PhasePhase 1
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment22
Start date1 November 2023
Primary completion16 April 2024
Estimated completion29 April 2024
Sites13 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Phathom Pharmaceuticals, Inc. — full company profile →

Who can join

Adults 6 to 11, any sex, with Gastroesophageal Reflux Disease. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Maximum Drug Concentration at Steady-state (Cmax,ss) of Vonoprazan Primary · Day 7: pre-dose, 0.5 to 1.5 hour and 2.5 to 3.5 hours post dose; Day 14: pre-dose, 1 to 2 hours and 3 to 4 hours post dose

Plasma pharmacokinetic (PK) parameters were estimated using a non-linear mixed effects model and were determined from the concentration-time data for all evaluable participants. Actual sampling times, rather than scheduled or nominal sampling times, were used in all computations using sampling time. Data presented based on collections on both Day 7 and Day 14.

GroupValue95% CI
Vonoprazan 10 mg16.29.31 – 27.1
Vonoprazan 20 mg42.110.1 – 72.7
Area Under the Plasma Concentration-time Curve During the Dosing Interval τ at Steady State (AUCτ,ss) of Vonoprazan Primary · Day 7: pre-dose, 0.5 to 1.5 hour and 2.5 to 3.5 hours post dose; Day 14: pre-dose, 1 to 2 hours and 3 to 4 hours post dose

Plasma PK parameters were estimated using a non-linear mixed effects model and were determined from the concentration-time data for all evaluable participants. Actual sampling times, rather than scheduled or nominal sampling times, were used in all computations using sampling time. Data presented based on collections on both Day 7 and Day 14.

GroupValue95% CI
Vonoprazan 10 mg88.351.7 – 121
Vonoprazan 20 mg25172.1 – 549
Apparent Oral Clearance (CL/F) at Steady State of Vonoprazan Primary · Day 7: pre-dose, 0.5 to 1.5 hour and 2.5 to 3.5 hours post dose; Day 14: pre-dose, 1 to 2 hours and 3 to 4 hours post dose

Oral PK parameters were estimated using a non-linear mixed effects model and were determined from the concentration-time data for all evaluable participants. Actual sampling times, rather than scheduled or nominal sampling times, were used in all computations using sampling time. Data presented based on collections on both Day 7 and Day 14.

GroupValue95% CI
Vonoprazan 10 mg12582.9 – 193
Vonoprazan 20 mg11836.4 – 278
Apparent Central Volume of Distribution (Vz/F) at Steady State of Vonoprazan Primary · Day 7: pre-dose, 0.5 to 1.5 hour and 2.5 to 3.5 hours post dose; Day 14: pre-dose, 1 to 2 hours and 3 to 4 hours post dose

Plasma PK parameters were estimated using a non-linear mixed effects model and were determined from the concentration-time data for all evaluable participants. Actual sampling times, rather than scheduled or nominal sampling times, were used in all computations using sampling time. Data presented based on collections on both Day 7 and Day 14.

GroupValue95% CI
Vonoprazan 10 mg491227 – 828
Vonoprazan 20 mg444164 – 1310

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to Day 28. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Vonoprazan 10 mg
Serious: 0/11 (0%)
Deaths: 0/11
Vonoprazan 20 mg
Serious: 0/11 (0%)
Deaths: 0/11
Other adverse events (4 terms — click to expand)

ReactionSystemVonoprazan 10 mgVonoprazan 20 mg
Tympanic membrane perforationEar and labyrinth disorders
VomitingGastrointestinal disorders
Otitis mediaInfections and infestations
Electrocardiogram QT prolongedInvestigations

Data from ClinicalTrials.gov NCT06106022 adverse events section.

Sponsor's own description

The aim of this study is to evaluate the pharmacokinetic (PK) profile of vonoprazan (10 or 20 mg once daily \[QD\]) in children ≥ 6 to \< 12 years of age who have symptomatic Gastroesophageal Reflux Disease (GERD).

Publications & conference data

2 peer-reviewed publications reference this trial (live from Europe PMC):

  1. The pharmacokinetics and safety of vonoprazan in adolescents and children with gastroesophageal reflux disease.
    Mulford DJ, Gremse DA, Chang YM, Leifke E, et al · · 2026 · PMID 41721637 · DOI 10.1002/jpn3.70368
  2. Abstract
    · 2025

Verify or expand the search:

Other trials of Vonoprazan

Trials testing the same drug.

Other recruiting trials for Gastroesophageal Reflux Disease

Currently open trials in the same condition.

Other Phathom Pharmaceuticals, Inc. trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT06106022.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing