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NCT05526521

A Study to Investigate the Pharmacokinetics and Safety of Dupilumab in Participants ≥2 Years to <12 Years of Age With Uncontrolled Chronic Spontaneous Urticaria (CSU) (LIBERTY-CSU CUPIDKids)

Completed Phase 3 Results posted Last updated 25 November 2025
What this trial tests

Phase 3 trial testing Dupilumab in Chronic Spontaneous Urticaria in 15 participants. Completed in 3 February 2025.

Timeline
25 August 2022
Primary endpoint
11 November 2024
3 February 2025

Quick facts

Lead sponsorSanofi
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment15
Start date25 August 2022
Primary completion11 November 2024
Estimated completion3 February 2025
Sites15 locations across Japan, Canada, United States

Drugs / interventions tested

Conditions studied

Sponsor

Sanofi — full company profile →

Who can join

Adults 2 to 11, any sex, with Chronic Spontaneous Urticaria. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Serum Concentration of Dupilumab at Weeks 12 and 24 Primary · Weeks 12 and 24

Blood samples were collected at specified timepoints to obtain dupilumab concentration.

Week 12
GroupValue95% CI
Dupilumab 200 mg Q4W67700
Dupilumab 300 mg Q4W105000
Dupilumab 300 mg Q4W, 600 mg Loading Dose45800± 12400
Dupilumab 200 mg Q2W, 400 mg Loading Dose91600± 23000
Week 24
GroupValue95% CI
Dupilumab 200 mg Q4W116000
Dupilumab 300 mg Q4W141000± 30100
Dupilumab 300 mg Q4W, 600 mg Loading Dose51100± 20100
Dupilumab 200 mg Q2W, 400 mg Loading Dose78500± 31600
Number of Participants With Treatment-emergent Adverse Events (TEAEs) and Treatment-emergent Serious Adverse Events (TESAEs) Secondary · From the first dose of study intervention (Day 1) up to end of follow-up, maximum up to 36 weeks

An adverse event (AE) was defined as any untoward medical occurrence in a participant or clinical trial participant, temporally associated with the use of study intervention, whether or not considered related to study intervention. Serious adverse event (SAE) was any untoward medical occurrence that at any dose: resulted in death, was life-threatening, required inpatient hospitalization or prolongation of existing hospitalization, resulted in persistent or significant disability/incapacity, was a congenital anomaly/birth defect or was an important medical event. TEAEs were defined as AEs that

TEAEs
GroupValue95% CI
Dupilumab 200 mg Q4W1
Dupilumab 300 mg Q4W2
Dupilumab 300 mg Q4W, 600 mg Loading Dose2
Dupilumab 200 mg Q2W, 400 mg Loading Dose7
TESAEs
GroupValue95% CI
Dupilumab 200 mg Q4W0
Dupilumab 300 mg Q4W0
Dupilumab 300 mg Q4W, 600 mg Loading Dose0
Dupilumab 200 mg Q2W, 400 mg Loading Dose0
Number of Participants With Anti-drug Antibodies (ADAs) to Dupilumab Secondary · From the first dose of study intervention (Day 1) up to end of follow-up, maximum up to 36 weeks

Blood samples were collected at specified timepoints and ADA samples were assayed using validated methods. Treatment-emergent ADA response was defined as a positive response in the ADA assay post first dose when baseline results were negative or missing. Number of participants with treatment-emergent ADA response is presented.

GroupValue95% CI
Dupilumab 200 mg Q4W0
Dupilumab 300 mg Q4W0
Dupilumab 300 mg Q4W, 600 mg Loading Dose0
Dupilumab 200 mg Q2W, 400 mg Loading Dose0
Change From Baseline in Children's Dermatology Life Quality Index (C-DLQI) in Participants Aged 4 Years to <12 Years at Week 24 Secondary · Baseline (Day 1) and Week 24

The C-DLQI assesses impact of skin disease on children's health-related quality of life (HRQoL) over the previous week, contains 10 questions related to symptoms feelings associated with disease, impact of disease on leisure, school or holidays, personal relationships, sleep, and side effects of treatment for the skin disease. All questions were scored on 4-point Likert scale:0 (not at all),1 (a little),2 (a lot),3 (very much). Total C-DLQI was calculated by summing the score of each question and ranged from 0 (no impact) to 30 (severe impact). Higher scores indicated poor HRQoL. Mean is prese

GroupValue95% CI
Dupilumab 200 mg Q4W-3.0
Dupilumab 300 mg Q4W-6.0
Dupilumab 300 mg Q4W, 600 mg Loading Dose-10.5± 3.5
Dupilumab 200 mg Q2W, 400 mg Loading Dose-7.3± 4.3
Change From Baseline in Infant's Dermatitis Quality of Life Index (IDQOL) in Participants Aged 2 Years to <4 Years at Week 24 Secondary · Baseline (Day 1) and Week 24

The IDQOL questionnaire is completed by child's caregiver/guardian with a recall period of 7 days;consists of 10 questions focusing on life quality index (LQI) scored on 4-point Likert scale. An additional question on dermatitis severity is scored on a 5-point Likert scale (0 \[none\] to 4 \[extremely severe\]); it is not considered for calculating total IDQOL. For LQI, score ranges are as follows: Questions 1, 5 to 10: 0 (none) to 3 (all the time/very much). Question 2: 0 (happy), 1 (slightly fretful), 2 (very fretful),3 (always crying). Question 3: 0 (0-15 minutes), 1 (15 minutes-1 hour), 2

GroupValue95% CI
Dupilumab 300 mg Q4W-3.0
Change From Baseline in Modified Urticaria Activity Score Over 7 Days (mUAS7) at Week 24 Secondary · Baseline (Day -7 to Day 1) and Week 24

A modified version of the UAS (mUAS) was used for the smaller body surface area of child and adolescent participants. The mUAS was derived from the sum of daily hives severity score (HSS) (ranging from 0 to 3 \[0 = absent; 1 = mild {1 to \<10 wheals/24 hours}; 2 = moderate: {10 to 30 wheals/24 hours}; and 3 = intense: {\>30 wheals/24 hours or large confluent areas of wheals}\]) and daily itch severity score (ISS) (ranging from 0 = none to 3 = intense). Daily mUAS total scores range from 0 to 6 (0 to 3 for ISS and 0 to 3 for HSS). Daily mUAS scores were summed over 7-day period to create total

GroupValue95% CI
Dupilumab 200 mg Q4W-8.0
Dupilumab 300 mg Q4W-21.4± 1.9
Dupilumab 300 mg Q4W, 600 mg Loading Dose-2.8± 1.8
Dupilumab 200 mg Q2W, 400 mg Loading Dose-7.8± 6.6
Change From Baseline in Itch Severity Score Over 7 Days (ISS7) at Week 24 Secondary · Baseline (Day -7 to Day 1) and Week 24

The ISS represents severity of itch on a scale ranging from 0 (none) to 3 (intense). The ISS7 score was the sum of daily ISS scores recorded by a participant at the same time each day over 7 days with an overall scale of 0 (no impact) to 21 (severe impact). Higher scores indicated greater intensity of itch. Mean is presented. Baseline was defined as sum of the 7 daily measurements obtained within the 7 days prior to first study intervention administration.

GroupValue95% CI
Dupilumab 200 mg Q4W-5.0
Dupilumab 300 mg Q4W-9.6± 3.7
Dupilumab 300 mg Q4W, 600 mg Loading Dose-1.6± 0.6
Dupilumab 200 mg Q2W, 400 mg Loading Dose-3.4± 3.2
Change From Baseline in Hive Severity Score Over 7 Days (HSS7) at Week 24 Secondary · Baseline (Day -7 to Day 1) and Week 24

The HSS7 score is the sum of daily HSS ranging from ranging from 0 to 3 (0 = absent; 1 = mild \[1 to \<10 wheals/24 hours\]; 2 = moderate \[10 to 30 wheals/24 hours\]; and 3 = intense: \[\>30 wheals/24 hours or large confluent areas of wheals\]) recorded by a participant at the same time of each day over 7 days with an overall scale of 0 (no hives) to 21 (severe hives). Higher scores indicate greater intensity of hives. Mean is presented. Baseline was defined as sum of the 7 daily measurements obtained within the 7 days prior to first study intervention administration.

GroupValue95% CI
Dupilumab 200 mg Q4W-3.0
Dupilumab 300 mg Q4W-11.8± 1.8
Dupilumab 300 mg Q4W, 600 mg Loading Dose-1.2± 1.2
Dupilumab 200 mg Q2W, 400 mg Loading Dose-4.4± 3.6

Adverse events — posted to ClinicalTrials.gov

Time frame: From the first dose of study intervention (Day 1) up to end of follow-up, maximum up to 36 weeks. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Dupilumab 200 mg Q4W
Serious: 0/1 (0%)
Deaths: 0/1
Dupilumab 300 mg Q4W
Serious: 0/4 (0%)
Deaths: 0/4
Dupilumab 300 mg Q4W, 600 mg Loading Dose
Serious: 0/2 (0%)
Deaths: 0/2
Dupilumab 200 mg Q2W, 400 mg Loading Dose
Serious: 0/8 (0%)
Deaths: 0/8
Other adverse events (34 terms — click to expand)

ReactionSystemDupilumab 200 mg Q4WDupilumab 300 mg Q4WDupilumab 300 mg Q4W, 600 …Dupilumab 200 mg Q2W, 400 …
NasopharyngitisInfections and infestations
Viral Upper Respiratory Tract InfectionInfections and infestations
HeadacheNervous system disorders
Covid-19Infections and infestations
Conjunctivitis BacterialInfections and infestations
FolliculitisInfections and infestations
Gastroenteritis ViralInfections and infestations
Hand-Foot-And-Mouth DiseaseInfections and infestations
HordeolumInfections and infestations
InfluenzaInfections and infestations
Otitis MediaInfections and infestations
PharyngitisInfections and infestations
Rhinovirus InfectionInfections and infestations
Subcutaneous AbscessInfections and infestations
Upper Respiratory Tract InfectionInfections and infestations
Viral RashInfections and infestations
Seasonal AllergyImmune system disorders
InsomniaPsychiatric disorders
MigraineNervous system disorders
Internal HaemorrhageVascular disorders
AsthmaRespiratory, thoracic and mediastinal disorders
RhinorrhoeaRespiratory, thoracic and mediastinal disorders
Abdominal DiscomfortGastrointestinal disorders
Abdominal Pain UpperGastrointestinal disorders
DiarrhoeaGastrointestinal disorders
Lip SwellingGastrointestinal disorders
VomitingGastrointestinal disorders
PsoriasisSkin and subcutaneous tissue disorders
Skin DiscolourationSkin and subcutaneous tissue disorders
FatigueGeneral disorders
Injection Site ReactionGeneral disorders
PyrexiaGeneral disorders
Swelling FaceGeneral disorders
Accidental OverdoseInjury, poisoning and procedural complications

Data from ClinicalTrials.gov NCT05526521 adverse events section.

Sponsor's own description

This was a multicenter, single-arm, 24-week treatment, Phase 3 study. The purpose of this study was to investigate the PK and safety of dupilumab in children diagnosed with CSU who remain symptomatic despite the use of H1-antihistamine treatment. Study details included: Screening: 2 to 4 weeks; The treatment duration was 24 weeks; Follow-up period: 12 weeks; The study duration was 38 to 40 weeks (including screening and follow-up); The number of study visits was 6.

Publications & conference data

5 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Dupilumab in Inflammatory Skin Diseases: A Systematic Review.
    Olbrich H, Sadik CD, Ludwig RJ, Thaçi D, et al · · 2023 · cited 67× · PMID 37189381 · DOI 10.3390/biom13040634
  2. Current and Emerging Therapies for Chronic Spontaneous Urticaria: A Narrative Review.
    Yosipovitch G, Biazus Soares G, Mahmoud O. · · 2023 · cited 20× · PMID 37386330 · DOI 10.1007/s13555-023-00972-6
  3. Advances in Biologic Therapies for Allergic Diseases: Current Trends, Emerging Agents, and Future Perspectives.
    Alska E, Łaszczych D, Napiórkowska-Baran K, Szymczak B, et al · · 2025 · cited 13× · PMID 40004611 · DOI 10.3390/jcm14041079
  4. Update on the Treatment of Chronic Spontaneous Urticaria.
    Kolkhir P, Fok JS, Kocatürk E, Li PH, et al · · 2025 · cited 10× · PMID 40074986 · DOI 10.1007/s40265-025-02170-4
  5. Neuro-immune interactions in urticaria:a pruritus-centric dissection
    Ke C, Ma N, Chen G, Yao Y, et al ·

Verify or expand the search:

Other trials of Dupilumab

Trials testing the same drug.

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Other Sanofi trials

Trials by the same sponsor.

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing