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NCT05239039

An Expanded Access Program in China to Provide Spesolimab to People With a Flare-up in Generalized Pustular Psoriasis Who Have no Other Treatment Options

Completed Phase 3 Results posted Last updated 20 October 2025
What this trial tests

Phase 3 trial testing spesolimab in Generalized Pustular Psoriasis in 39 participants. Completed in 17 July 2023.

Timeline
15 March 2022
Primary endpoint
17 July 2023
17 July 2023

Quick facts

Lead sponsorBoehringer Ingelheim
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment39
Start date15 March 2022
Primary completion17 July 2023
Estimated completion17 July 2023
Sites12 locations across China

Drugs / interventions tested

Conditions studied

Sponsor

Boehringer Ingelheim — full company profile →

Who can join

Adults 18 to 75, any sex, with Generalized Pustular Psoriasis. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Occurrence of Treatment Emergent Adverse Events (AEs) Primary · From initial drug administration to: end of study treatment + residual effect period or end of study visit. Up to 16 weeks for the single dose group and up to 17 weeks for the double dose group.

This outcome measured the number of patients with any treatment-emergent adverse event (AE). Treatment-emergent AEs are untoward medical events that appear or worsen during treatment.

GroupValue95% CI
Spesolimab Single Dose Treatment18
Spesolimab Double Dose Treatment12
Occurrence of Treatment Emergent Serious Adverse Events (SAEs) Secondary · From initial drug administration to: end of study treatment + residual effect period or end of study visit. Up to 16 weeks for the single dose group and up to 17 weeks for the double dose group.

This outcome measured the number of patients with serious adverse events (SAEs). SAEs are untoward medical occurrences that result in death, are life threatening, require inpatient hospitalisation, require prolongation of existing hospitalisation, result in persistent or significant disability/incapacity, result in a congenital anomaly/birth defect, or are deemed serious for any other medically important reason.

GroupValue95% CI
Spesolimab Single Dose Treatment1
Spesolimab Double Dose Treatment2
Occurrence of Treatment Emergent Adverse Events of Special Interest (AESIs) Secondary · From initial drug administration to: end of study treatment + residual effect period or end of study visit. Up to 16 weeks for the single dose group and up to 17 weeks for the double dose group.

This outcome measured the number of patients with any treatment-emergent adverse event of special interest (AESIs). AESIs relates to any specific AE that has been identified at the project level as being of particular concern for prospective safety monitoring and safety assessment within this program. Potential severe DILIs (drug-induced liver injury), systemic hypersensitivity reactions, severe infections, opportunistic and mycobacterium tuberculosis infections, and peripheral neuropathy were considered as AESIs.

GroupValue95% CI
Spesolimab Single Dose Treatment1
Spesolimab Double Dose Treatment1

Adverse events — posted to ClinicalTrials.gov

Time frame: From initial drug administration to: end of study treatment + residual effect period or end of study visit. Up to 16 weeks for the single dose group and up to 17 weeks for the double dose group.. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Spesolimab Single Dose Treatment
Serious: 1/24 (4%)
Deaths: 0/24
Spesolimab Double Dose Treatment
Serious: 2/15 (13%)
Deaths: 0/15

Serious adverse events (4 terms)

ReactionSystemSpesolimab Single Dose Tre…Spesolimab Double Dose Tre…
COVID-19Infections and infestations
PneumoniaInfections and infestations
Respiratory failureRespiratory, thoracic and mediastinal disorders
Pustular psoriasisSkin and subcutaneous tissue disorders
Other adverse events (22 terms — click to expand)

ReactionSystemSpesolimab Single Dose Tre…Spesolimab Double Dose Tre…
COVID-19Infections and infestations
Upper respiratory tract infectionInfections and infestations
PyrexiaGeneral disorders
HyperuricaemiaMetabolism and nutrition disorders
HypoproteinaemiaMetabolism and nutrition disorders
PruritusSkin and subcutaneous tissue disorders
AnaemiaBlood and lymphatic system disorders
NasopharyngitisInfections and infestations
Urinary tract infectionInfections and infestations
HypokalaemiaMetabolism and nutrition disorders
RashSkin and subcutaneous tissue disorders
UrticariaSkin and subcutaneous tissue disorders
LymphadenitisBlood and lymphatic system disorders
MyringitisInfections and infestations
Tinea versicolourInfections and infestations
Blood albumin decreasedInvestigations
Neutrophil count increasedInvestigations
Prealbumin decreasedInvestigations
White blood cell count increasedInvestigations
Psoriatic arthropathyMusculoskeletal and connective tissue disorders
EczemaSkin and subcutaneous tissue disorders
Excessive granulation tissueSkin and subcutaneous tissue disorders

Most-reported serious reactions: COVID-19, Pneumonia, Respiratory failure, Pustular psoriasis.

Data from ClinicalTrials.gov NCT05239039 adverse events section.

Sponsor's own description

This Expanded Access Program in China is open to people with a serious skin disease called Generalized Pustular Psoriasis (GPP). This program provides a medicine called spesolimab to people with a GPP flare-up who have no alternative treatment options. This means that no therapy exists and participation in a clinical study is not possible. Participants get a single infusion of spesolimab into a vein. They can get another spesolimab infusion one week after the first infusion if the doctors think it is helpful. Participants are in the program for about 4 months and visit the study site about 5 times. Participants who benefit from the treatment during that time may repeat the treatment in case they experience a new GPP flare-up. The doctors regularly check participants' health and take note of any unwanted effects.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Spesolimab: First Approval.
    Blair HA. · · 2022 · cited 61× · PMID 36418672 · DOI 10.1007/s40265-022-01801-4
  2. IL-1 Family Cytokines in Inflammatory Dermatoses: Pathogenetic Role and Potential Therapeutic Implications.
    Iznardo H, Puig L. · · 2022 · cited 44× · PMID 36012744 · DOI 10.3390/ijms23169479
  3. Immune cells in the epithelial immune microenvironment of psoriasis: emerging therapeutic targets.
    Li L, Lu J, Liu J, Wu J, et al · · 2023 · cited 26× · PMID 38239345 · DOI 10.3389/fimmu.2023.1340677
  4. Spesolimab for the Treatment of Generalized Pustular Psoriasis.
    Bernardo D, Thaçi D, Torres T. · · 2024 · cited 22× · PMID 38114719 · DOI 10.1007/s40265-023-01988-0
  5. A Review of the Clinical Trial Landscape in Psoriasis: An Update for Clinicians.
    Drakos A, Vender R. · · 2022 · cited 15× · PMID 36319883 · DOI 10.1007/s13555-022-00840-9
  6. Spesolimab for generalized pustular psoriasis: a review of two key clinical trials supporting initial US regulatory approval.
    Gwillim EC, Nichols AJ. · · 2024 · cited 8× · PMID 39104539 · DOI 10.3389/fimmu.2024.1359481
  7. Current Treatments for Generalized Pustular Psoriasis: A Narrative Summary of a Systematic Literature Search.
    Puig L, Fujita H, Thaçi D, Zheng M, et al · · 2024 · cited 8× · PMID 39088126 · DOI 10.1007/s13555-024-01230-z
  8. New and Emerging Treatments for Generalized Pustular Psoriasis: Focus on IL-36 Receptor Inhibitors.
    Vilaça J, Yilmaz O, Torres T. · · 2024 · cited 5× · PMID 39065604 · DOI 10.3390/pharmaceutics16070908

Verify or expand the search:

Other trials of spesolimab

Trials testing the same drug.

Other recruiting trials for Generalized Pustular Psoriasis

Currently open trials in the same condition.

Other Boehringer Ingelheim trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT05239039.

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