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NCT05200247

An Expanded Access Trial in Japan to Provide Spesolimab to People With a Flare-up in Generalized Pustular Psoriasis Who Have no Other Treatment Options

Completed Phase 3 Results posted Last updated 25 February 2025
What this trial tests

Phase 3 trial testing spesolimab in Generalized Pustular Psoriasis in 11 participants. Completed in 20 March 2023.

Timeline
17 February 2022
Primary endpoint
20 March 2023
20 March 2023

Quick facts

Lead sponsorBoehringer Ingelheim
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment11
Start date17 February 2022
Primary completion20 March 2023
Estimated completion20 March 2023
Sites9 locations across Japan

Drugs / interventions tested

Conditions studied

Sponsor

Boehringer Ingelheim — full company profile →

Who can join

Adults 18 to 75, any sex, with Generalized Pustular Psoriasis. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Occurrence of Treatment Emergent Adverse Events (TEAEs) Primary · From first administration of study drug until last administration of study drug + 16 weeks of follow up, up to 6.3 months.

Number of patients with any treatment emergent adverse events (TEAEs) is reported. An adverse events (AE) was defined as any untoward medical occurrence in a patient or clinical investigation subject administered a medicinal product and which does not necessarily have to have a causal relationship with this treatment. An AE that started before first drug intake and deteriorated under treatment were also considered as 'treatment-emergent'.

GroupValue95% CI
Spesolimab 900 mg i.v. SD7
Occurrence of Treatment Emergent Serious Adverse Events (SAEs) Secondary · From first administration of study drug until last administration of study drug + 16 weeks of follow up, up to 6.3 months.

Number of patients with treatment emergent serious adverse events (SAEs) is reported. A serious adverse event (SAE) was defined as any AE which fulfils at least one of the following criteria: * results in death, * is life-threatening, which refers to an event in which the patient was at risk of death at the time of the event; * requires inpatient hospitalisation or prolongation of existing hospitalisation, * results in persistent or significant disability or incapacity, * is a congenital anomaly / birth defect, * is deemed serious for any other reason if it is an important medical event when

GroupValue95% CI
Spesolimab 900 mg i.v. SD0
Occurrence of Treatment Emergent Adverse Events of Special Interest (AESIs) Secondary · From first administration of study drug until last administration of study drug + 16 weeks of follow up, up to 6.3 months.

Number of patients with treatment emergent adverse events of special interest (AESIs) is reported. The term adverse events of special interest (AESI) relates to any specific adverse event (AE) that has been identified at the project level as being of particular concern for prospective safety monitoring and safety assessment within this trial, e.g. the potential for AEs based on knowledge from other compounds in the same class. The following are considered as AESIs: * Potential Severe Drug Induced Liver Injury (DILI) * Systemic hypersensitivity reactions including infusion reactions and anap

GroupValue95% CI
Spesolimab 900 mg i.v. SD0

Adverse events — posted to ClinicalTrials.gov

Time frame: From first administration of study drug until last administration of study drug + 16 weeks of follow up, up to 6.3 months.. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Spesolimab 900 mg i.v. SD
Serious: 0/11 (0%)
Deaths: 0/11
Other adverse events (12 terms — click to expand)

ReactionSystemSpesolimab 900 mg i.v. SD
Pustular psoriasisSkin and subcutaneous tissue disorders
ConstipationGastrointestinal disorders
Chest painGeneral disorders
Face oedemaGeneral disorders
MalaiseGeneral disorders
PeriodontitisInfections and infestations
WoundInjury, poisoning and procedural complications
Coronavirus test positiveInvestigations
Transaminases increasedInvestigations
HeadacheNervous system disorders
PollakiuriaRenal and urinary disorders
AcneSkin and subcutaneous tissue disorders

Data from ClinicalTrials.gov NCT05200247 adverse events section.

Sponsor's own description

This Expanded Access trial in Japan is open to people with a serious skin disease called Generalized Pustular Psoriasis (GPP). This program provides a medicine called spesolimab to people with a GPP flare-up who have no alternative treatment options. Participants get a single infusion of spesolimab into a vein. They can get another spesolimab infusion one week after the first infusion if the doctors think it is helpful. Participants are in the program for about 4 months and visit the study site about 5 to 6 times. The doctors regularly check participants' health and take note of any unwanted effects.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Spesolimab: First Approval.
    Blair HA. · · 2022 · cited 61× · PMID 36418672 · DOI 10.1007/s40265-022-01801-4
  2. IL-1 Family Cytokines in Inflammatory Dermatoses: Pathogenetic Role and Potential Therapeutic Implications.
    Iznardo H, Puig L. · · 2022 · cited 44× · PMID 36012744 · DOI 10.3390/ijms23169479
  3. Immune cells in the epithelial immune microenvironment of psoriasis: emerging therapeutic targets.
    Li L, Lu J, Liu J, Wu J, et al · · 2023 · cited 26× · PMID 38239345 · DOI 10.3389/fimmu.2023.1340677
  4. Spesolimab for the Treatment of Generalized Pustular Psoriasis.
    Bernardo D, Thaçi D, Torres T. · · 2024 · cited 22× · PMID 38114719 · DOI 10.1007/s40265-023-01988-0
  5. A Review of the Clinical Trial Landscape in Psoriasis: An Update for Clinicians.
    Drakos A, Vender R. · · 2022 · cited 15× · PMID 36319883 · DOI 10.1007/s13555-022-00840-9
  6. Spesolimab for generalized pustular psoriasis: a review of two key clinical trials supporting initial US regulatory approval.
    Gwillim EC, Nichols AJ. · · 2024 · cited 8× · PMID 39104539 · DOI 10.3389/fimmu.2024.1359481
  7. Current Treatments for Generalized Pustular Psoriasis: A Narrative Summary of a Systematic Literature Search.
    Puig L, Fujita H, Thaçi D, Zheng M, et al · · 2024 · cited 8× · PMID 39088126 · DOI 10.1007/s13555-024-01230-z
  8. New and Emerging Treatments for Generalized Pustular Psoriasis: Focus on IL-36 Receptor Inhibitors.
    Vilaça J, Yilmaz O, Torres T. · · 2024 · cited 5× · PMID 39065604 · DOI 10.3390/pharmaceutics16070908

Verify or expand the search:

Other trials of spesolimab

Trials testing the same drug.

Other recruiting trials for Generalized Pustular Psoriasis

Currently open trials in the same condition.

Other Boehringer Ingelheim trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

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