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NCT04799158

A Study to Evaluate the Efficacy and Safety of Vonoprazan Compared to Placebo in Participants With Symptomatic Non-Erosive Gastroesophageal Reflux Disease

Completed Phase 2 Results posted Last updated 4 January 2023
What this trial tests

Phase 2 trial testing Vonoprazan in Non-Erosive Gastro-Esophageal Reflux Disease in 458 participants. Completed in 17 January 2022.

Timeline
25 March 2021
Primary endpoint
16 December 2021
17 January 2022

Quick facts

Lead sponsorPhathom Pharmaceuticals, Inc.
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingdouble
Primary purposetreatment
Enrollment458
Start date25 March 2021
Primary completion16 December 2021
Estimated completion17 January 2022
Sites63 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Phathom Pharmaceuticals, Inc. — full company profile →

Who can join

18 and older, any sex, with Non-Erosive Gastro-Esophageal Reflux Disease or Heartburn. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percentage of Evaluable Heartburn Episodes Completely Relieved Within 3 Hours and With No Further Heartburn Reported for 24 Hours After Taking Study Drug Primary · On-Demand Treatment Period: Day 1 to Day 42

An evaluable heartburn episode was an episode for which study drug was taken and for which the participant completed at least one entry in the heartburn episode diary. For a heartburn episode to be considered completely relieved, a participant must not have taken rescue antacid within 3 hours of taking study drug. For sustained relief, complete relief must have been accompanied by 24 hours without another heartburn episode after taking study drug.

GroupValue95% CI
Vonoprazan 10 mg: On-Demand Treatment Period56.0
Vonoprazan 20 mg: On-Demand Treatment Period60.6
Vonoprazan 40 mg: On-Demand Treatment Period70.0
Placebo: On-Demand Treatment Period27.3
Percentage of Evaluable Heartburn Episodes Completely Relieved Within 3 Hours After Taking Study Drug Secondary · On-Demand Treatment Period: Day 1 to Day 42

An evaluable heartburn episode was an episode for which study drug was taken and for which the participant completed at least one entry in the heartburn episode diary. For a heartburn episode to be considered completely relieved, a participant must not have taken rescue antacid within 3 hours of taking study drug.

GroupValue95% CI
Vonoprazan 10 mg: On-Demand Treatment Period72.1
Vonoprazan 20 mg: On-Demand Treatment Period65.7
Vonoprazan 40 mg: On-Demand Treatment Period79.6
Placebo: On-Demand Treatment Period41.9
Percentage of Evaluable Heartburn Episodes for Each Participant That Are Completely Relieved Within 3 Hours and With No Further Heartburn Reported for 24 Hours After Taking Study Drug Secondary · On-Demand Treatment Period: Day 1 to Day 42

An evaluable heartburn episode was an episode for which study drug was taken and for which the participant completed at least one entry in the heartburn episode diary. For a heartburn episode to be considered completely relieved, a participant must not have taken rescue antacid within 3 hours of taking study drug. For sustained relief, complete relief must have been accompanied by 24 hours without another heartburn episode after taking study drug.

GroupValue95% CI
Vonoprazan 10 mg: On-Demand Treatment Period60.08± 38.452
Vonoprazan 20 mg: On-Demand Treatment Period60.78± 37.458
Vonoprazan 40 mg: On-Demand Treatment Period71.99± 28.894
Placebo: On-Demand Treatment Period47.77± 40.998
Mean Number of Tablets of Rescue Antacid Taken Per Day Over the On-Demand Treatment Period Secondary · On-Demand Treatment Period: Day 1 to Day 42
GroupValue95% CI
Vonoprazan 10 mg: On-Demand Treatment Period0.1± 0.21
Vonoprazan 20 mg: On-Demand Treatment Period0.2± 0.29
Vonoprazan 40 mg: On-Demand Treatment Period0.1± 0.26
Placebo: On-Demand Treatment Period0.5± 0.87
Percentage of Participants With Complete Relief of Heartburn Within 3 Hours After the First Episode and With No Further Heartburn Reported for 24 Hours After Taking Study Drug Secondary · On-Demand Treatment Period: Day 1 to Day 42

An evaluable heartburn episode was an episode for which study drug was taken and for which the participant completed at least one entry in the heartburn episode diary. For a heartburn episode to be considered completely relieved, a participant must not have taken rescue antacid within 3 hours of taking study drug. For sustained relief, complete relief must have been accompanied by 24 hours without another heartburn episode after taking study drug.

GroupValue95% CI
Vonoprazan 10 mg: On-Demand Treatment Period56.5
Vonoprazan 20 mg: On-Demand Treatment Period61.9
Vonoprazan 40 mg: On-Demand Treatment Period62.8
Placebo: On-Demand Treatment Period60.5
Percentage of Days Study Drug Was Taken Over the On-Demand Treatment Period Secondary · On-Demand Treatment Period: Day 1 to Day 42
GroupValue95% CI
Vonoprazan 10 mg: On-Demand Treatment Period21.93± 19.241
Vonoprazan 20 mg: On-Demand Treatment Period20.75± 16.950
Vonoprazan 40 mg: On-Demand Treatment Period21.01± 17.302
Placebo: On-Demand Treatment Period22.15± 23.266
Percentage of 24-Hour Heartburn-Free Days Over the On-Demand Treatment Period Secondary · On-Demand Treatment Period: Day 1 to Day 42

A 24-hour heartburn-free day was defined as a day having no heartburn among all diary entries for that day. The percentage of 24-hour heartburn-free days was calculated using all days with at least 1 evening or morning diary entry during the treatment period of this phase.

GroupValue95% CI
Vonoprazan 10 mg: On-Demand Treatment Period74.95± 21.410
Vonoprazan 20 mg: On-Demand Treatment Period73.57± 21.465
Vonoprazan 40 mg: On-Demand Treatment Period74.01± 22.277
Placebo: On-Demand Treatment Period71.22± 28.867

Adverse events — posted to ClinicalTrials.gov

Time frame: Run-In Period: Day 1 to Day 28; On-Demand Treatment: Day 1 to Day 49. Reporting threshold: 2%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Run-In Period
Serious: 4/457 (1%)
Deaths: 0/457
Vonoprazan 10 mg: On-Demand Treatment Period
Serious: 0/49 (0%)
Deaths: 0/49
Vonoprazan 20 mg: On-Demand Treatment Period
Serious: 0/49 (0%)
Deaths: 0/49
Vonoprazan 40 mg: On-Demand Treatment Period
Serious: 0/48 (0%)
Deaths: 0/48
Placebo: On-Demand Treatment Period
Serious: 0/47 (0%)
Deaths: 0/47

Serious adverse events (4 terms)

ReactionSystemRun-In PeriodVonoprazan 10 mg: On-Deman…Vonoprazan 20 mg: On-Deman…Vonoprazan 40 mg: On-Deman…Placebo: On-Demand Treatme…
Acute myocardial infarctionCardiac disorders
Myocardial infarctionCardiac disorders
Anaphylactic reactionImmune system disorders
Suicidal ideationPsychiatric disorders
Other adverse events (41 terms — click to expand)

ReactionSystemRun-In PeriodVonoprazan 10 mg: On-Deman…Vonoprazan 20 mg: On-Deman…Vonoprazan 40 mg: On-Deman…Placebo: On-Demand Treatme…
DiarrhoeaGastrointestinal disorders
Abdominal distensionGastrointestinal disorders
NauseaGastrointestinal disorders
FlatulenceGastrointestinal disorders
Urinary tract infectionInfections and infestations
COVID-19Infections and infestations
NasopharyngitisInfections and infestations
Back painMusculoskeletal and connective tissue disorders
ThrombocytosisBlood and lymphatic system disorders
Atrioventricular block first degreeCardiac disorders
Abdominal painGastrointestinal disorders
MelaenaGastrointestinal disorders
Chest discomfortGeneral disorders
Breast abscessInfections and infestations
CystitisInfections and infestations
GastroenteritisInfections and infestations
Otitis mediaInfections and infestations
SinusitisInfections and infestations
Upper respiratory tract infectionInfections and infestations
Ligament sprainInjury, poisoning and procedural complications
Meniscus injuryInjury, poisoning and procedural complications
Nail avulsionInjury, poisoning and procedural complications
Post-traumatic painInjury, poisoning and procedural complications
Road traffic accidentInjury, poisoning and procedural complications
Blood alkaline phosphatase increasedInvestigations
Blood glucose increasedInvestigations
Gamma-glutamyltransferase increasedInvestigations
Liver function test increasedInvestigations
Urine analysis abnormalInvestigations
HyperglycaemiaMetabolism and nutrition disorders
ArthralgiaMusculoskeletal and connective tissue disorders
Muscle spasmsMusculoskeletal and connective tissue disorders
Musculoskeletal painMusculoskeletal and connective tissue disorders
OsteoarthritisMusculoskeletal and connective tissue disorders
DysgeusiaNervous system disorders
MigraineNervous system disorders
SciaticaNervous system disorders
Chronic obstructive pulmonary diseaseRespiratory, thoracic and mediastinal disorders
CoughRespiratory, thoracic and mediastinal disorders
Dermatitis contactSkin and subcutaneous tissue disorders

Most-reported serious reactions: Acute myocardial infarction, Myocardial infarction, Anaphylactic reaction, Suicidal ideation.

Data from ClinicalTrials.gov NCT04799158 adverse events section.

Sponsor's own description

The primary objectives of this study are to assess the efficacy of vonoprazan (10 mg, 20 mg, and 40 mg On-Demand) compared to placebo (On-Demand) in relief of episodic heartburn over 6 weeks in participants with symptomatic non-erosive gastroesophageal reflux disease (NERD), and to assess the safety of vonoprazan (10 mg, 20 mg, and 40 mg On-Demand) compared to placebo (On-Demand) in participants with symptomatic NERD.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Randomised clinical trial: Efficacy and safety of on-demand vonoprazan versus placebo for non-erosive reflux disease.
    Fass R, Vaezi M, Sharma P, Yadlapati R, et al · · 2023 · cited 29× · PMID 37750406 · DOI 10.1111/apt.17728

Verify or expand the search:

Other trials of Vonoprazan

Trials testing the same drug.

Other recruiting trials for Non-Erosive Gastro-Esophageal Reflux Disease

Currently open trials in the same condition.

Other Phathom Pharmaceuticals, Inc. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04799158.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing