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NCT04746235

Venetoclax and ASTX727 for the Treatment of Relapsed, Refractory, or Newly Diagnosed Acute Myeloid Leukemia

Active, enrolled Phase 2 Last updated 12 March 2026
What this trial tests

Phase 2 trial testing Decitabine and Cedazuridine in Acute Myeloid Leukemia in 85 participants. Participants enrolled and being followed up; not accepting new ones.

Timeline
22 February 2021
Primary endpoint
31 October 2026
31 October 2026

Quick facts

Lead sponsorM.D. Anderson Cancer Center
PhasePhase 2
StatusActive, enrolled
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment85
Start date22 February 2021
Primary completion31 October 2026
Estimated completion31 October 2026
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

M.D. Anderson Cancer Center — full company profile →

Who can join

18 and older, any sex, with Acute Myeloid Leukemia or Recurrent Acute Myeloid Leukemia. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This phase II trial studies the possible benefits of venetoclax and ASTX727 in treating patients with acute myeloid leukemia that has come back (relapsed) or does not respond to treatment (refractory), or elderly patients with newly diagnosed acute myeloid leukemia who are not candidates for intensive chemotherapy. Venetoclax may help block the formation of growths that may become cancer. ASTX727 is the combination of a fixed dose of 2 drugs, cedazuridine and decitabine. Cedazuridine may slow down how fast decitabine is broken down by the body, and decitabine may block abnormal cells or cancer cells from growing. Giving venetoclax and ASTX727 may help to control the disease.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Venetoclax resistance: mechanistic insights and future strategies.
    Ong F, Kim K, Konopleva MY. · · 2022 · cited 79× · PMID 35800373 · DOI 10.20517/cdr.2021.125
  2. Ten-day decitabine with venetoclax versus intensive chemotherapy in relapsed or refractory acute myeloid leukemia: A propensity score-matched analysis.
    Maiti A, DiNardo CD, Qiao W, Kadia TM, et al · · 2021 · cited 33× · PMID 34343352 · DOI 10.1002/cncr.33814
  3. Cedazuridine/decitabine: from preclinical to clinical development in myeloid malignancies.
    Patel AA, Cahill K, Saygin C, Odenike O. · · 2021 · cited 29× · PMID 33904891 · DOI 10.1182/bloodadvances.2020002929
  4. How We Incorporate Venetoclax in Treatment Regimens for Acute Myeloid Leukemia.
    Maiti A, Konopleva MY. · · 2022 · cited 19× · PMID 35072368 · DOI 10.1097/ppo.0000000000000567
  5. Oral decitabine and cedazuridine plus venetoclax for older or unfit patients with acute myeloid leukaemia: a phase 2 study.
    Bazinet A, Garcia-Manero G, Short N, Alvarado Y, et al · · 2024 · cited 16× · PMID 38452788 · DOI 10.1016/s2352-3026(24)00033-4
  6. Targeting Apoptosis in AML: Where Do We Stand?
    Krawiec K, Strzałka P, Czemerska M, Wiśnik A, et al · · 2022 · cited 14× · PMID 36291779 · DOI 10.3390/cancers14204995
  7. Clinical activity, pharmacokinetics, and pharmacodynamics of oral hypomethylating agents for myelodysplastic syndromes/neoplasms and acute myeloid leukemia: A multidisciplinary review.
    Haumschild R, Kennerly-Shah J, Barbarotta L, Zeidan AM. · · 2024 · cited 12× · PMID 38509812 · DOI 10.1177/10781552241238979
  8. Combination of a New Oral Demethylating Agent, OR2100, and Venetoclax for Treatment of Acute Myeloid Leukemia.
    Kamachi K, Ureshino H, Watanabe T, Yoshida-Sakai N, et al · · 2023 · cited 12× · PMID 36860654 · DOI 10.1158/2767-9764.crc-22-0259

Verify or expand the search:

Other trials of Decitabine and Cedazuridine

Trials testing the same drug.

Other recruiting trials for Acute Myeloid Leukemia

Currently open trials in the same condition.

Other M.D. Anderson Cancer Center trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

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