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NCT04562792

Low Dose Daunorubicin in Pediatric Relapsed/Refractory Acute Leukemia

Completed Phase 2 Results posted Last updated 28 June 2023
What this trial tests

Phase 2 trial testing Daunorubicin in Relapsed Pediatric ALL in 1 participant. Completed in 30 June 2022.

Timeline
8 May 2020
Primary endpoint
30 June 2022
30 June 2022

Quick facts

Lead sponsorChildren's Mercy Hospital Kansas City
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment1
Start date8 May 2020
Primary completion30 June 2022
Estimated completion30 June 2022
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Children's Mercy Hospital Kansas City

Who can join

Adults 1 to 21, any sex, with Relapsed Pediatric ALL or Relapsed Pediatric AML. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Incidence of Low Dose Daunorubicin Feasbility as Assessed by Absolute Blast Count Primary · 24 months

Feasibility failure due to progressive leukemia is defined as a rise in absolute blast count (ABC) of \>10,000/day on two consecutive days that continues to increase \>10,000/day after starting hydroxyurea.

GroupValue95% CI
Patients With Relapsed/Refractory ALL and AML0
Patients With Relapsed/Refractory ALL and AML1
Incidence of Low Dose Daunorubicin Feasbility as Assessed by Extramedullary Leukemia Progression Primary · 24 months

Low dose daunorubicin will also be deemed not feasible if there is evidence of progression of extramedullary leukemia such progression of chloroma or leukemia cutis. or if the patient experiences uncontrollable nausea and/or vomiting.

GroupValue95% CI
Patients With Relapsed/Refractory ALL and AML0
Patients With Relapsed/Refractory ALL and AML1
Incidence of Low Dose Daunorubicin Feasbility as Assessed by Patient Symptoms Primary · 24 months

Low dose daunorubicin will also be deemed not feasible if the patient experiences uncontrollable nausea and/or vomiting.

GroupValue95% CI
Patients With Relapsed/Refractory ALL and AML0
Patients With Relapsed/Refractory ALL and AML1
Pharmacokinetic Parameters of Low Dose Daunorubicin in Children With Relapsed/Refractory AML and ALL as Assessed by Maximum Concentration. Secondary · 24 months

Serial daunorubicin levels for evaluation of maximum concentration will be drawn prior to infusion and at 5, 20 and 40 minutes and at hours 1,2,4,8 and 24 post infusion.

GroupValue95% CI
Patients With Relapsed/Refractory ALL and AML18.7
Pharmacokinetic Parameters of Low Dose Daunorubicin in Children With Relapsed/Refractory AML and ALL as Assessed by Time at Maximum Concentration. Secondary · 24 months

Serial daunorubicin levels for evaluation of time at maximum concentration will be drawn prior to infusion and at 5, 20 and 40 minutes and hours 1,2,4,8 and 24 post infusion.

GroupValue95% CI
Patients With Relapsed/Refractory ALL and AML0.33333
Pharmacokinetic Parameters of Low Dose Daunorubicin in Children With Relapsed/Refractory AML and ALL as Assessed by Area Under the Curve. Secondary · 24 months

Serial daunorubicin levels for evaluation of exposure by measuring area under the curve will be drawn prior to infusion and at 5, 20 and 40 minutes and hours 1,2,4,8 and 24 post infusion.

GroupValue95% CI
Patients With Relapsed/Refractory ALL and AML20.889865
Pharmacokinetic Parameters of Low Dose Daunorubicin in Children With Relapsed/Refractory AML and ALL as Assessed by Elimination Half-life Secondary · 24 months

Serial daunorubicin levels for evaluation of exposure by measuring elimination half-life will be drawn prior to infusion and at 5, 20 and 40 minutes and hours 1,2,4,8 and 24 post infusion.

GroupValue95% CI
Patients With Relapsed/Refractory ALL and AML1.8588

Sponsor's own description

In this pilot study, eligible pediatric patients will be treated with 5 consecutive days of low dose daunorubicin. All patients who receive low dose daunorubicin will be evaluated daily for potential toxicity during those 5 days. Once the patient has received 5 doses of daunorubicin, subsequent therapy will be at the discretion of the primary oncology team.

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. The genesis and evolution of acute myeloid leukemia stem cells in the microenvironment: From biology to therapeutic targeting.
    Chen Y, Li J, Xu L, Găman MA, et al · · 2022 · cited 32× · PMID 36163119 · DOI 10.1038/s41420-022-01193-0
  2. An Overview of Advances in Rare Cancer Diagnosis and Treatment.
    Christyani G, Carswell M, Qin S, Kim W. · · 2024 · cited 17× · PMID 38256274 · DOI 10.3390/ijms25021201
  3. Wnt Signaling Pathway: Biological Function, Diseases, and Therapeutic Interventions.
    Jin X, Wang J, Cao R, Jiang D. · · 2026 · PMID 41541657 · DOI 10.1002/mco2.70580

Verify or expand the search:

Other trials of Daunorubicin

Trials testing the same drug.

Other recruiting trials for Relapsed Pediatric ALL

Currently open trials in the same condition.

Other Children's Mercy Hospital Kansas City trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04562792.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing