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NCT04353752

Observational Trial of the Longitudinal Effects of CFTR Modulator Drugs

Completed Last updated 13 April 2026
What this trial tests

trial in Cystic Fibrosis in 58 participants. Completed in 26 July 2023.

Timeline
16 September 2019
Primary endpoint
12 January 2021
26 July 2023

Quick facts

Lead sponsorNational Jewish Health
StatusCompleted
Study typeOBSERVATIONAL
Enrollment58
Start date16 September 2019
Primary completion12 January 2021
Estimated completion26 July 2023
Sites1 location across United States

Conditions studied

Sponsor

National Jewish Health — full company profile →

Who can join

18 and older, any sex, with Cystic Fibrosis. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

CF patients enrolled in this protocol will be recruited from patients followed by the Adult CF Program at National Jewish Health. Patients will be selected based on planned use of a CFTR modulator by their primary physician. No patient will be started on (or will switch) CFTR modulator agents for the purpose of the study. After enrollment, biological samples may be collected at two different time points prior to treatment initiation. One set of samples will be collected at baseline health prior to CFTR modulator initiation or change. A second set of samples will be obtained in subjects at the time of acute pulmonary exacerbation, if one occurs prior to CFTR modulator initiation or change. Post CFTR modulator initiation study assessments will be obtained at least one month after starting treatment and continue up to 2 times a year (including during pulmonary exacerbations), in order to document longitudinal effects of therapies and changes in inflammatory biology over time. At the time of each biological sampling, blood, sputum sample, urine, and a quality of life assessment will be acquired in all enrolled subjects. In addition to demographic data, clinical data, such as quantitative microbiology and simple spirometry will be recorded at the time of sample collection.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Lipocalin 2-not only a biomarker: a study of current literature and systematic findings of ongoing clinical trials.
    Asaf S, Maqsood F, Jalil J, Sarfraz Z, et al · · 2023 · cited 38× · PMID 36529828 · DOI 10.1007/s12026-022-09352-2

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Other recruiting trials for Cystic Fibrosis

Currently open trials in the same condition.

Other National Jewish Health trials

Trials by the same sponsor.

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