Last reviewed · How we verify
Cystic Fibrosis
Approved treatments
- Trikafta (Copackaged) · Vertex Pharms Inc
Trikafta works by correcting the faulty protein that causes cystic fibrosis, allowing the body to produce normal amounts of mucus. - Mannitol · Baxter
Osmotic diuretic that elevates glomerular filtrate osmolarity to inhibit tubular water reabsorption. - Alyftrek · Vertex Pharms Inc
Alyftrek potentiates the CFTR protein to facilitate chloride ion flow into cells. - Alyftrek · Vertex Pharms Inc
Alyftrek potentiates the CFTR protein to facilitate chloride ion flow into cells. - Aridol Kit · Baxter
Mannitol works by drawing water into the bloodstream from surrounding tissues, increasing urine production and reducing fluid accumulation in the body. - Pulmozyme · Roche
Pulmozyme breaks down DNA in the airways to reduce mucus viscosity.
Competitive intelligence
For the full treatment-landscape CI brief — marketed leaders side-by-side, pipeline by phase, recent regulatory actions, sponsor landscape: