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NCT03770403: ADAPT+

A Safety and Tolerability Study of ARGX-113 in Patients With Myasthenia Gravis Who Have Generalized Muscle Weakness.

Completed Phase 3 Results posted Last updated 14 July 2023
What this trial tests

Phase 3 trial testing ARGX-113 in Generalized Myasthenia Gravis in 151 participants. Completed in 30 June 2022.

Timeline
1 March 2019
Primary endpoint
23 June 2022
30 June 2022

Quick facts

Lead sponsorargenx
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment151
Start date1 March 2019
Primary completion23 June 2022
Estimated completion30 June 2022
Sites52 locations across Georgia, Denmark, France, Italy, Japan, Netherlands, Russia, Belgium

Drugs / interventions tested

Conditions studied

Sponsor

argenx — full company profile →

Who can join

18 and older, any sex, with Generalized Myasthenia Gravis. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Participants With Treatment-Emergent Adverse Events (TEAEs), Treatment-Emergent Serious AEs, TEAEs Leading to Study Drug Discontinuation and Fatal TEAE in AChR-Positive Participants Primary · TEAEs were collected from the start of first administered study treatment (Day 1) up to end of follow-up, approximately up to 3 years

An AE was any untoward medical occurrence in a clinical study participant, temporally associated with the use of study treatment, whether or not considered related to the study treatment. Any clinically significant abnormal laboratory test results (hematology, clinical chemistry, or urinalysis) or other safety assessments (electrocardiogram \[ECG\], radiological scans, vital signs measurements) were collected as AEs. All AEs starting on or after first dose administered and until completion of participant's last visit were considered as TEAEs. A serious AE (SAE) was any AE that resulted in deat

TEAE
GroupValue95% CI
Efgartigimod92
Treatment-emergent SAE
GroupValue95% CI
Efgartigimod28
TEAEs leading to study drug discontinuation
GroupValue95% CI
Efgartigimod10
Fatal TEAE
GroupValue95% CI
Efgartigimod4
Number of Participants With TEAEs, Treatment-Emergent SAEs, TEAEs Leading to Study Drug Discontinuation and Fatal TEAE in the Overall Population Secondary · TEAEs were collected from the start of first administered study treatment (Day 1) up to end of follow-up, approximately up to 3 years

Overall population included both AChR-Ab seropositive and AChR-Ab seronegative participants. An AE was any untoward medical occurrence in a clinical study participant, temporally associated with the use of study treatment, whether or not considered related to the study treatment. Any clinically significant abnormal laboratory test results (hematology, clinical chemistry, or urinalysis) or other safety assessments (ECG, radiological scans, vital signs measurements) were collected as AEs. All AEs starting on or after first dose administered and until completion of participant's last visit were c

TEAE
GroupValue95% CI
Efgartigimod124
Treatment-emergent SAE
GroupValue95% CI
Efgartigimod36
TEAEs leading to study drug discontinuation
GroupValue95% CI
Efgartigimod12
Fatal TEAE
GroupValue95% CI
Efgartigimod5

Adverse events — posted to ClinicalTrials.gov

Time frame: TEAEs were collected from the start of first administered study treatment (Day 1) up to end of follow-up, approximately up to 3 years. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Efgartigimod
Serious: 36/145 (25%)
Deaths: 5/145

Serious adverse events (44 terms)

ReactionSystemEfgartigimod
Myasthenia gravisNervous system disorders
Cardiac failure congestiveCardiac disorders
COVID-19Infections and infestations
COVID-19 pneumoniaInfections and infestations
PneumoniaInfections and infestations
Myasthenia gravis crisisNervous system disorders
Acute respiratory failureRespiratory, thoracic and mediastinal disorders
AnaemiaBlood and lymphatic system disorders
Acute myocardial infarctionCardiac disorders
ArrhythmiaCardiac disorders
Atrial fibrillationCardiac disorders
Defect conduction intraventricularCardiac disorders
Retinal detachmentEye disorders
DiarrhoeaGastrointestinal disorders
Irritable bowel syndromeGastrointestinal disorders
DeathGeneral disorders
DysenteryInfections and infestations
Pneumonia escherichiaInfections and infestations
Pseudomonal sepsisInfections and infestations
Septic shockInfections and infestations
Urinary tract infectionInfections and infestations
Infusion related reactionInjury, poisoning and procedural complications
Spinal compression fractureInjury, poisoning and procedural complications
SARS-CoV-2 test positiveInvestigations
Type 1 diabetes mellitusMetabolism and nutrition disorders
Other adverse events (10 terms — click to expand)

ReactionSystemEfgartigimod
HeadacheNervous system disorders
NasopharyngitisInfections and infestations
COVID-19Infections and infestations
DiarrhoeaGastrointestinal disorders
Urinary tract infectionInfections and infestations
ArthralgiaMusculoskeletal and connective tissue disorders
PyrexiaGeneral disorders
NauseaGastrointestinal disorders
Oropharyngeal painRespiratory, thoracic and mediastinal disorders
HypertensionVascular disorders

Most-reported serious reactions: Myasthenia gravis, Cardiac failure congestive, COVID-19, COVID-19 pneumonia, Pneumonia, Myasthenia gravis crisis, Acute respiratory failure, Anaemia.

Data from ClinicalTrials.gov NCT03770403 adverse events section.

Sponsor's own description

This is a Long-Term, Single-Arm, Open-Label, Multicenter Phase 3 follow-on trial of the ARGX-113-1704 study to evaluate the safety and tolerability of ARGX-113 in patients with gMG. Patients who have completed at least 1 cycle of treatment and at least 1 year of trial ARGX-113-1705 and have started Part B are eligible to enroll in the open-label trial ARGX-113-2002 to receive efgartigimod by SC administration.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT): a multicentre, randomised, placebo-controlled, phase 3 trial.
    Howard JF, Bril V, Vu T, Karam C, et al · · 2021 · cited 505× · PMID 34146511 · DOI 10.1016/s1474-4422(21)00159-9
  2. The therapeutic age of the neonatal Fc receptor.
    Pyzik M, Kozicky LK, Gandhi AK, Blumberg RS. · · 2023 · cited 166× · PMID 36726033 · DOI 10.1038/s41577-022-00821-1
  3. Efgartigimod: First Approval.
    Heo YA. · · 2022 · cited 108× · PMID 35179720 · DOI 10.1007/s40265-022-01678-3
  4. Long-term safety, tolerability, and efficacy of efgartigimod (ADAPT+): interim results from a phase 3 open-label extension study in participants with generalized myasthenia gravis.
    Howard JF, Bril V, Vu T, Karam C, et al · · 2023 · cited 45× · PMID 38318236 · DOI 10.3389/fneur.2023.1284444
  5. Antibody Therapies in Autoimmune Neuromuscular Junction Disorders: Approach to Myasthenic Crisis and Chronic Management.
    Vanoli F, Mantegazza R. · · 2022 · cited 26× · PMID 35165857 · DOI 10.1007/s13311-022-01181-3
  6. New and emerging treatments for myasthenia gravis.
    DeHart-McCoyle M, Patel S, Du X. · · 2023 · cited 25× · PMID 37560511 · DOI 10.1136/bmjmed-2022-000241
  7. Monoclonal Antibody-Based Therapies for Myasthenia Gravis.
    Alabbad S, AlGaeed M, Sikorski P, Kaminski HJ. · · 2020 · cited 23× · PMID 32915379 · DOI 10.1007/s40259-020-00443-w
  8. New and Emerging Biological Therapies for Myasthenia Gravis: A Focussed Review for Clinical Decision-Making.
    Gerischer L, Doksani P, Hoffmann S, Meisel A. · · 2025 · cited 18× · PMID 39869260 · DOI 10.1007/s40259-024-00701-1

Verify or expand the search:

Other trials of ARGX-113

Trials testing the same drug.

Other recruiting trials for Generalized Myasthenia Gravis

Currently open trials in the same condition.

Other argenx trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03770403.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing