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NCT03515837

Study of Pemetrexed + Platinum Chemotherapy With or Without Pembrolizumab (MK-3475) in Adults With Tyrosine Kinase Inhibitor- (TKI)-Resistant Epidermal Growth Factor Receptor- (EGFR)-Mutated Metastatic Non-squamous Non-small Cell Lung Cancer (NSCLC) (MK-3475-789/KEYNOTE-789)

Completed Phase 3 Results posted Last updated 22 November 2024
What this trial tests

Phase 3 trial testing pembrolizumab in Non-small Cell Lung Cancer in 492 participants. Completed in 2 October 2023.

Timeline
29 June 2018
Primary endpoint
17 January 2023
2 October 2023

Quick facts

Lead sponsorMerck Sharp & Dohme LLC
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment492
Start date29 June 2018
Primary completion17 January 2023
Estimated completion2 October 2023
Sites158 locations across France, Hong Kong, Italy, Japan, Sweden, Taiwan, United Kingdom, Germany

Drugs / interventions tested

Conditions studied

Sponsor

Merck Sharp & Dohme LLC — full company profile →

Who can join

18 and older, any sex, with Non-small Cell Lung Cancer. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Progression-free Survival (PFS) Per Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1) Primary · Up to ~40 months

PFS is defined as the time from randomization to the first documented progressive disease (PD) or death due to any cause, whichever occurs first. PFS was assessed by blinded independent central review (BICR) using RECIST 1.1. Per RECIST 1.1, PD is defined as at least a 20% increase in the sum of diameters of target lesions. In addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 mm. Note: The appearance of one or more new lesions is also considered PD. The PFS presented was analyzed using the product-limit (Kaplan-Meier) method for censored

GroupValue95% CI
Pembro + Pemetrexed + Chemo5.65.5 – 5.8
Placebo + Pemetrexed + Chemo5.55.4 – 5.6
Overall Survival (OS) Primary · Up to ~51 months

OS is defined as the time from randomization to death due to any cause. Participants without documented death at the time of the final analysis will be censored at the date of the last follow-up. The OS presented was analyzed using the product-limit (Kaplan-Meier) method for censored data.

GroupValue95% CI
Pembro + Pemetrexed + Chemo15.913.7 – 18.8
Placebo + Pemetrexed + Chemo14.712.7 – 17.1
Objective Response Rate (ORR) Per RECIST 1.1 Secondary · Up to ~51 months

ORR was assessed by BICR using RECIST 1.1. ORR is defined as the percentage of participants in the analysis population who experience a Complete Response (CR: Disappearance of all target lesions) or a Partial Response (PR: At least a 30% decrease in the sum of diameters of target lesions, taking as reference the baseline sum diameters) per RECIST 1.1. The ORR for participants is presented.

GroupValue95% CI
Pembro + Pemetrexed + Chemo29.023.4 – 35.1
Placebo + Pemetrexed + Chemo27.121.7 – 33.1
Duration of Response (DOR) Per RECIST 1.1 Secondary · Up to ~51 months

DOR was assessed by BICR using RECIST 1.1. For participants who experience a response of CR or PR, DOR is defined as the time from the earliest date of qualifying response until earliest date of PD or death from any cause, whichever comes first. The DOR presented was analyzed using the product-limit (Kaplan-Meier) method for censored data.

GroupValue95% CI
Pembro + Pemetrexed + Chemo6.35.9 – 8.3
Placebo + Pemetrexed + Chemo5.64.4 – 6.3
Change From Baseline in European Organization for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire-Core 30 (QLQ-C30) Global Health Status (Item 29) and Quality of Life (Item 30) Combined Score Secondary · Baseline and Week 18

The EORTC QLQ-C30 is a questionnaire to assess the overall quality of life of cancer patients. Participant responses to the questions regarding Global Health Status (GHS; "How would you rate your overall health during the past week?") and Quality of Life (QoL; "How would you rate your overall quality of life during the past week?") are each scored on a 7-point scale (1=Very poor to 7=Excellent). The two raw scores were averaged into a combined score, then normalized using linear transformation so each participant's score ranged from 0 to 100 (0=Worst overall health/quality of life and 100=Best

GroupValue95% CI
Pembro + Pemetrexed + Chemo-0.46-3.17 – 2.25
Placebo + Pemetrexed + Chemo-2.05-4.74 – 0.64
Time to True Deterioration (TTD) in the EORTC Questionnaire Composite Endpoint of Cough, Chest Pain or Dyspnea Secondary · Baseline and up to ~51 months

TTD is the time from baseline to first onset of 10 points or more deterioration from baseline with confirmation by the subsequent visit of 10 points or more deterioration from baseline in the composite endpoint of cough \[EORTC QLQ-Lung Cancer Module 13 (LC13) Item 1; How much did you cough?\], chest pain \[EORTC QLQ-LC13 Item 10; Have you had pain in your chest?\], or dyspnea \[EORTC QLQ-C30 Item 8; Were you short of breath?\]. Individual responses are given on a 4-point scale (1=Not at all; 4=Very much), with a lower score indicating a better outcome. The TTD was analyzed using the product-l

GroupValue95% CI
Pembro + Pemetrexed + ChemoNA10.05 – NA
Placebo + Pemetrexed + Chemo17.976.67 – NA
Percentage of Participants Who Experienced an Adverse Event (AE) Secondary · Up to ~44 months

An AE is defined as any unfavorable and unintended change in the structure, function, or chemistry of the body temporally associated with the use of the study treatment, whether or not considered related to the use of study treatment. The percentage of participants who experienced an AE is presented.

GroupValue95% CI
Pembro + Pemetrexed + Chemo97.6
Placebo + Pemetrexed + Chemo98.0
Percentage of Participants Who Discontinued Study Treatment Due to AEs Secondary · Up to ~41 months

An AE is defined as any unfavorable and unintended change in the structure, function, or chemistry of the body temporally associated with the use of the study treatment, whether or not considered related to the use of study treatment. The percentage of participants who discontinued study treatment due to an adverse event is presented.

GroupValue95% CI
Pembro + Pemetrexed + Chemo19.2
Placebo + Pemetrexed + Chemo17.1

Adverse events — posted to ClinicalTrials.gov

Time frame: Death and Adverse Events up to ~59 months.. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Pembro + Pemetrexed + Chemo
Serious: 86/245 (35%)
Deaths: 219/245
Placebo + Pemetrexed + Chemo
Serious: 70/246 (28%)
Deaths: 186/247
Placebo + Pemetrexed + Chemo Switched Over to Pembro Monotherapy
Serious: 8/50 (16%)
Deaths: 44/50

Serious adverse events (126 terms)

ReactionSystemPembro + Pemetrexed + ChemoPlacebo + Pemetrexed + ChemoPlacebo + Pemetrexed + Che…
AnaemiaBlood and lymphatic system disorders
PneumoniaInfections and infestations
Platelet count decreasedInvestigations
Pleural effusionRespiratory, thoracic and mediastinal disorders
VomitingGastrointestinal disorders
PyrexiaGeneral disorders
Neutrophil count decreasedInvestigations
White blood cell count decreasedInvestigations
Cerebrovascular accidentNervous system disorders
Febrile neutropeniaBlood and lymphatic system disorders
SepsisInfections and infestations
Alanine aminotransferase increasedInvestigations
Aspartate aminotransferase increasedInvestigations
Decreased appetiteMetabolism and nutrition disorders
NauseaGastrointestinal disorders
General physical health deteriorationGeneral disorders
Cerebral infarctionNervous system disorders
Pericardial effusionCardiac disorders
DiarrhoeaGastrointestinal disorders
FatigueGeneral disorders
Device related infectionInfections and infestations
DiverticulitisInfections and infestations
InfectionInfections and infestations
Urinary tract infectionInfections and infestations
MyositisMusculoskeletal and connective tissue disorders
Other adverse events (41 terms — click to expand)

ReactionSystemPembro + Pemetrexed + ChemoPlacebo + Pemetrexed + ChemoPlacebo + Pemetrexed + Che…
Neutrophil count decreasedInvestigations
AnaemiaBlood and lymphatic system disorders
NauseaGastrointestinal disorders
White blood cell count decreasedInvestigations
ConstipationGastrointestinal disorders
Decreased appetiteMetabolism and nutrition disorders
FatigueGeneral disorders
Alanine aminotransferase increasedInvestigations
Aspartate aminotransferase increasedInvestigations
Platelet count decreasedInvestigations
VomitingGastrointestinal disorders
CoughRespiratory, thoracic and mediastinal disorders
PyrexiaGeneral disorders
HeadacheNervous system disorders
AstheniaGeneral disorders
Oedema peripheralGeneral disorders
Back painMusculoskeletal and connective tissue disorders
DiarrhoeaGastrointestinal disorders
Blood creatinine increasedInvestigations
Weight decreasedInvestigations
MalaiseGeneral disorders
DizzinessNervous system disorders
InsomniaPsychiatric disorders
ArthralgiaMusculoskeletal and connective tissue disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
Gamma-glutamyltransferase increasedInvestigations
Upper respiratory tract infectionInfections and infestations
Urinary tract infectionInfections and infestations
HyperglycaemiaMetabolism and nutrition disorders
Chest painGeneral disorders
Pain in extremityMusculoskeletal and connective tissue disorders
PruritusSkin and subcutaneous tissue disorders
Lymphocyte count decreasedInvestigations
HypokalaemiaMetabolism and nutrition disorders
DysgeusiaNervous system disorders
Abdominal painGastrointestinal disorders
HypothyroidismEndocrine disorders
RashSkin and subcutaneous tissue disorders
HypertensionVascular disorders
HyperthyroidismEndocrine disorders

Most-reported serious reactions: Anaemia, Pneumonia, Platelet count decreased, Pleural effusion, Vomiting, Pyrexia, Neutrophil count decreased, White blood cell count decreased.

Data from ClinicalTrials.gov NCT03515837 adverse events section.

Sponsor's own description

The purpose of this study is to evaluate the efficacy and safety of pemetrexed plus platinum chemotherapy (carboplatin or cisplatin) with or without pembrolizumab (MK-3475; KEYTRUDA®) in the treatment of adults with the following types of tyrosine kinase inhibitor (TKI)-resistant, epidermal growth factor receptor (EGFR)-mutated, metastatic non-squamous non-small cell lung cancer (NSCLC) tumors: 1) TKI-failures (including osimertinib \[TAGRISSO®\] failure) with T790M-negative mutation tumors, 2) T790M-positive mutation tumors with prior exposure to osimertinib, and 3) first-line osimertinib failure regardless of T790M mutation status. The primary study hypotheses are that the combination of pembrolizumab plus chemotherapy has superior efficacy compared to saline placebo plus chemotherapy in terms of: 1) Progression-free Survival (PFS) per Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1) based on blinded independent central review, and 2) Overall Survival (OS). This study will be considered to have met its success criteria if the combination of pembrolizumab plus chemotherapy is superior to saline placebo plus chemotherapy in terms of PFS or OS. Upon study completion, participants are discontinued and may be enrolled in a pembrolizumab extension study, if available.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Immunotherapy in Non-Small Cell Lung Cancer: Facts and Hopes.
    Doroshow DB, Sanmamed MF, Hastings K, Politi K, et al · · 2019 · cited 532× · PMID 30824587 · DOI 10.1158/1078-0432.ccr-18-1538
  2. Third-generation EGFR and ALK inhibitors: mechanisms of resistance and management.
    Cooper AJ, Sequist LV, Lin JJ. · · 2022 · cited 382× · PMID 35534623 · DOI 10.1038/s41571-022-00639-9
  3. Therapeutic strategies for EGFR-mutated non-small cell lung cancer patients with osimertinib resistance.
    Fu K, Xie F, Wang F, Fu L. · · 2022 · cited 271× · PMID 36482474 · DOI 10.1186/s13045-022-01391-4
  4. Mechanisms and management of 3rd‑generation EGFR‑TKI resistance in advanced non‑small cell lung cancer (Review).
    He J, Huang Z, Han L, Gong Y, et al · · 2021 · cited 232× · PMID 34558640 · DOI 10.3892/ijo.2021.5270
  5. Targeted therapy in advanced non-small cell lung cancer: current advances and future trends.
    Majeed U, Manochakian R, Zhao Y, Lou Y. · · 2021 · cited 193× · PMID 34238332 · DOI 10.1186/s13045-021-01121-2
  6. The cutting-edge progress of immune-checkpoint blockade in lung cancer.
    Zhou F, Qiao M, Zhou C. · · 2021 · cited 177× · PMID 33177696 · DOI 10.1038/s41423-020-00577-5
  7. Optimizing the sequencing of tyrosine kinase inhibitors (TKIs) in epidermal growth factor receptor (EGFR) mutation-positive non-small cell lung cancer (NSCLC).
    Gelatti ACZ, Drilon A, Santini FC. · · 2019 · cited 172× · PMID 31568888 · DOI 10.1016/j.lungcan.2019.09.017
  8. Phase III KEYNOTE-789 Study of Pemetrexed and Platinum With or Without Pembrolizumab for Tyrosine Kinase Inhibitor‒Resistant, <i>EGFR</i>-Mutant, Metastatic Nonsquamous Non-Small Cell Lung Cancer.
    Yang JC, Lee DH, Lee JS, Fan Y, et al · · 2024 · cited 158× · PMID 39173098 · DOI 10.1200/jco.23.02747

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