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NCT03386266
Biomarkers and Validation of Selected Outcome Measures (CMTNSmod)
trial in Charcot-Marie-Tooth Disease, Type IA in 156 participants. Completed in 30 September 2019.
30 September 2019
Quick facts
| Lead sponsor | University Medical Center Goettingen |
|---|---|
| Status | Completed |
| Study type | OBSERVATIONAL |
| Enrollment | 156 |
| Start date | 11 August 2017 |
| Primary completion | 30 September 2019 |
| Estimated completion | 30 September 2019 |
| Sites | 1 location across Germany |
Conditions studied
- Charcot-Marie-Tooth Disease, Type IA — all drugs for Charcot-Marie-Tooth Disease, Type IA →
Sponsor
University Medical Center Goettingen
Who can join
Adults 3 to 65, any sex, with Charcot-Marie-Tooth Disease, Type IA. Patients with the condition only — healthy volunteers not accepted.
Sponsor's own description
CMT is a rare disease for which novel treatments are being developed. Evaluation of intervention efficacy is hampered by slow progression and lack of sensitive outcome measures. Primary goal of the project is to identify and validate RNA and protein derived biomarkers in blood of CMT patients for selected outcome measures over 2 years. The investigators expect to develop more responsive outcome measures and circulating biomarkers to improve assessment of intervention efficacy in forthcoming therapeutic trials.
Publications & conference data
No peer-reviewed publications indexed yet for this trial. Completed trials usually publish results within 12-18 months.
Verify or expand the search:
- PubMed search for NCT03386266
- Europe PMC full search
- ASCO Meeting Library
- ESMO Meeting Library
- bioRxiv preprints
- medRxiv preprints
- Google Scholar
Related trials
Other recruiting trials for Charcot-Marie-Tooth Disease, Type IA
Currently open trials in the same condition.
- NCT05902351 — Natural History Study for Charcot Marie Tooth Disease · recruiting
Other University Medical Center Goettingen trials
Trials by the same sponsor.
- NCT07505498 — Screening for Supportive Care Needs of Oncological Patients and Professionals - Evaluation of a Short PRO-question Set · recruiting
- NCT07008677 — Oral Health Awareness and Status Among Professional Musicians in German Orchestras · completed
- NCT07529041 — Real-time Acoustic Biofeedback for Enhancing Fixation Stability: A Proof-of-concept Study to Improve Ophthalmic Imaging · NA · enrolling by invitation
- NCT06921863 — This Study Aims to Quantify Decisional Regret as Well as Quality of Life in Patients With Low- to High-risk Cancer and H · not yet recruiting
- NCT07476365 — A Multi-omic Approach to the Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A Disease (CMT1A) · recruiting
Verify against primary sources
- ClinicalTrials.gov — authoritative US registry record
- WHO ICTRP — international registry index
- EU Clinical Trials Register
- Sponsor press releases (Google)
- Trial protocol + status: ClinicalTrials.gov NCT03386266 (US National Library of Medicine, public domain)
- Drug + disease cross-links: matched in real time against Drug Landscape's normalised drug + company + condition tables
- Sponsor: as reported to ClinicalTrials.gov by University Medical Center Goettingen
- Last refreshed: 5 November 2020
Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03386266.
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing