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NCT01776840

A Study of the Bruton's Tyrosine Kinase Inhibitor Ibrutinib Given in Combination With Bendamustine and Rituximab in Patients With Newly Diagnosed Mantle Cell Lymphoma

Completed Phase 3 Results posted Last updated 8 July 2025
What this trial tests

Phase 3 trial testing Bendamustine in Mantle Cell Lymphoma in 523 participants. Completed in 24 June 2024.

Timeline
16 May 2013
Primary endpoint
30 June 2021
24 June 2024

Quick facts

Lead sponsorJanssen Research & Development, LLC
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment523
Start date16 May 2013
Primary completion30 June 2021
Estimated completion24 June 2024
Sites201 locations across Japan, Taiwan, Ireland, Poland, South Korea, Netherlands, Russia, Belgium

Drugs / interventions tested

Conditions studied

Sponsor

Janssen Research & Development, LLC — full company profile →

Who can join

65 and older, any sex, with Mantle Cell Lymphoma. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Progression-free Survival (PFS) Primary · Up to 97 months

Progression-free survival (PFS) was defined as the interval between the date of randomization to the date of disease progression (PD) or relapse from complete response (CR) or death, whichever was first reported. Disease assessments were based on the 2007 Revised Response Criteria for Malignant Lymphoma. PD was defined as any new lesion or increase by 50 percent (%) of previously involved sites from nadir (PD criteria: Appearance of new nodal lesion 1.5 centimeters \[cm\] in any axis, 50% increase in sum of product of diameters \[SPD\] of greater than \[\>\] 1 node or 50% increase in longest d

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)52.943.7 – 71.0
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)80.661.9 – NA
Overall Survival Secondary · From randomization (Day -3) up to 121 months

Overall survival was defined as the time from the date of randomization to the date of the participant's death. Kaplan-Meier estimate was used.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)95.986.1 – 115.3
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)104.381.1 – NA
Complete Response Rate Secondary · Up to 97 months

Complete response (CR) rate was defined as the percentage of participants who achieve CR (based on investigator assessment) on or prior to the initiation of subsequent anticancer therapy. Criteria for CR: disappearance of all evidence of disease; mass of any size permitted if positron emission tomography (PET) negative; regression to normal size on computed tomography (CT); spleen and liver: not palpable, nodules disappeared; bone marrow: infiltrate cleared on repeat biopsy.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)57.6
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)65.5
Time-to-Next Treatment Secondary · Up to 97 months

Time-to-next treatment was measured from the date of randomization to the start date of any anti-mantle cell lymphoma (anti-MCL) treatment subsequent to the study treatment.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)92.071.5 – NA
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)NANA – NA
Percentage of Participants With Overall Response Secondary · Up to 97 months

Percentage of participants with overall response was defined as the portion of participants who achieved CR or PR. Criteria for CR: disappearance of all evidence of disease; mass of any size permitted if PET negative; regression to normal size on CT; spleen and liver: not palpable, nodules disappeared; bone marrow: infiltrate cleared on repeat biopsy. Criteria for PR: greater than or equal to (\>=) 50% decrease in sum of the diameter of all target lesions compared with baseline, in absence of new lesions or unequivocal progression of non-target lesions.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)88.5
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)89.7
Minimal Residual Disease (MRD)-Negative Response Rate Secondary · Up to 97 months

Minimal residual disease negative rate was defined as the percentage of participants with a best overall response of CR with MRD-negative disease status (that is, \<5 mantle cell lymphoma \[MCL\] cell per 10,000 leukocytes for detection using the MRD assay), as assessed by flow cytometry of a bone marrow and/or peripheral blood sample.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)56.5
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)62.1
Time to Worsening (TTW) in the Lymphoma (Lym) Subscale of the Functional Assessment of Cancer Therapy-Lymphoma (FACT-Lym) Questionnaire Secondary · Up to 97 months

Time to worsening in the Lymphoma subscale of the FACT-Lym, defined as the interval from the date of randomization to the start date of worsening of participant symptoms. Worsening was defined by a 5-point decrease from baseline, death, or a missing assessment due to being "too ill", whichever occurred first. FACT-Lym Lymphoma subscale contains 15 questions, scores from 0 to 4 for each question (higher the worse). Lymphoma subscale score was the total of reverse scores, ranged 0 to 60. Higher scores indicated a better quality of life.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)22.29.3 – 34.0
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)17.48.3 – 27.6
Duration of Response (DoR) Secondary · Up to 97 months

Duration of Response (DoR) was defined as the interval between the date of initial documentation of a response including PR and the date of first documented evidence of PD or death

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)63.547 – 76.9
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)8164.2 – NA
Duration of Complete Response (DoCR) Secondary · Up to 97 months

Duration of complete response (DoCR) was defined as the interval between the date of initial documentation of a CR and the date of first documented evidence of PD or death whichever occurs first.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)78.165.6 – NA
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)NA81.7 – NA
Time to Response Secondary · Up to 97 months

Time to response was defined as the interval between the date of randomization and the date of initial documentation of a response.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)2.791.9 – 11.2
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)2.792.1 – 10.1
Number of Participants With Treatment-emergent Adverse Events (TEAEs) Secondary · Placebo + BR (Treatment A): From first dose of study treatment (Day 1) up to 100.1 months; Ibrutinib + BR (Treatment B): From first dose of study treatment (Day 1) up to 117.2 months

Number of participants with TEAEs were reported. An AE was any untoward medical occurrence in a clinical study participant administered a medicinal (investigational or non investigational) product. An AE does not necessarily have a causal relationship with the intervention. Treatment-emergent adverse events were defined as adverse events with onset or worsening on or after date of first dose of study treatment up to and including 30 days after date of last dose of study medication, or the initiation of subsequent anticancer therapy, whichever is earlier.

GroupValue95% CI
Placebo + Bendamustine and Rituximab (BR) (Treatment A)257
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)259
Oral Plasma Clearance (CL/F) of Ibrutinib Secondary · Pre-dose on Day 2 of Cycles 1, 2 and 3; and 1, 2 and 4 hours post-dose on Day 2 of Cycles 1 and 2

CL/F was defined as apparent total systemic clearance of ibrutinib after extravascular administration. Cl/F of Ibrutinib was determined using population pharmacokinetics (PopPK modeling).

GroupValue95% CI
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)1123± 4.83

Adverse events — posted to ClinicalTrials.gov

Time frame: All-cause mortality: From randomization (Day -3) up to 121 months; SAEs and Non SAEs: Placebo + BR (Treatment A): From first dose of study treatment (Day 1) up to 100.1 months; Ibrutinib + BR (Treatment B): From first dose of study treatment (Day 1) up to 117.2 months. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Placebo + Bendamustine and Rituximab (BR) (Treatment A)
Serious: 157/260 (60%)
Deaths: 129/262
Ibrutinib + Bendamustine and Rituximab (BR) (Treatment B)
Serious: 201/259 (78%)
Deaths: 120/261

Serious adverse events (365 terms)

ReactionSystemPlacebo + Bendamustine and…Ibrutinib + Bendamustine a…
PneumoniaInfections and infestations
PyrexiaGeneral disorders
Febrile NeutropeniaBlood and lymphatic system disorders
Atrial FibrillationCardiac disorders
SepsisInfections and infestations
CellulitisInfections and infestations
DiarrhoeaGastrointestinal disorders
Covid-19 PneumoniaInfections and infestations
Acute Kidney InjuryRenal and urinary disorders
BronchitisInfections and infestations
Urinary Tract InfectionInfections and infestations
Pleural EffusionRespiratory, thoracic and mediastinal disorders
Myocardial InfarctionCardiac disorders
AnaemiaBlood and lymphatic system disorders
Cardiac ArrestCardiac disorders
VomitingGastrointestinal disorders
Lower Respiratory Tract InfectionInfections and infestations
Respiratory Tract InfectionInfections and infestations
DehydrationMetabolism and nutrition disorders
SyncopeNervous system disorders
Chronic Obstructive Pulmonary DiseaseRespiratory, thoracic and mediastinal disorders
Respiratory FailureRespiratory, thoracic and mediastinal disorders
RashSkin and subcutaneous tissue disorders
Rash Maculo-PapularSkin and subcutaneous tissue disorders
Acute Myocardial InfarctionCardiac disorders
Other adverse events (93 terms — click to expand)

ReactionSystemPlacebo + Bendamustine and…Ibrutinib + Bendamustine a…
DiarrhoeaGastrointestinal disorders
NeutropeniaBlood and lymphatic system disorders
NauseaGastrointestinal disorders
RashSkin and subcutaneous tissue disorders
PyrexiaGeneral disorders
CoughRespiratory, thoracic and mediastinal disorders
AnaemiaBlood and lymphatic system disorders
FatigueGeneral disorders
Upper Respiratory Tract InfectionInfections and infestations
ConstipationGastrointestinal disorders
ThrombocytopeniaBlood and lymphatic system disorders
VomitingGastrointestinal disorders
PruritusSkin and subcutaneous tissue disorders
Decreased AppetiteMetabolism and nutrition disorders
PneumoniaInfections and infestations
Oedema PeripheralGeneral disorders
ArthralgiaMusculoskeletal and connective tissue disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
Neutrophil Count DecreasedInvestigations
Platelet Count DecreasedInvestigations
HeadacheNervous system disorders
ChillsGeneral disorders
HypokalaemiaMetabolism and nutrition disorders
Back PainMusculoskeletal and connective tissue disorders
HypertensionVascular disorders
BronchitisInfections and infestations
Urinary Tract InfectionInfections and infestations
SinusitisInfections and infestations
White Blood Cell Count DecreasedInvestigations
MyalgiaMusculoskeletal and connective tissue disorders
Atrial FibrillationCardiac disorders
Lymphocyte Count DecreasedInvestigations
EpistaxisRespiratory, thoracic and mediastinal disorders
AstheniaGeneral disorders
Abdominal PainGastrointestinal disorders
InsomniaPsychiatric disorders
NasopharyngitisInfections and infestations
LeukopeniaBlood and lymphatic system disorders
Herpes ZosterInfections and infestations
ConjunctivitisInfections and infestations

Most-reported serious reactions: Pneumonia, Pyrexia, Febrile Neutropenia, Atrial Fibrillation, Sepsis, Cellulitis, Diarrhoea, Covid-19 Pneumonia.

Data from ClinicalTrials.gov NCT01776840 adverse events section.

Sponsor's own description

The purpose of this study is to evaluate the efficacy and safety of ibrutinib given in combination with bendamustine and rituximab in patients 65 years of age or older with newly diagnosed mantle cell lymphoma.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Inhibitors targeting Bruton's tyrosine kinase in cancers: drug development advances.
    Wen T, Wang J, Shi Y, Qian H, et al · · 2021 · cited 182× · PMID 33122850 · DOI 10.1038/s41375-020-01072-6
  2. Ibrutinib plus Bendamustine and Rituximab in Untreated Mantle-Cell Lymphoma.
    Wang ML, Jurczak W, Jerkeman M, Trotman J, et al · · 2022 · cited 158× · PMID 35657079 · DOI 10.1056/nejmoa2201817
  3. Outcomes in 370 patients with mantle cell lymphoma treated with ibrutinib: a pooled analysis from three open-label studies.
    Rule S, Dreyling M, Goy A, Hess G, et al · · 2017 · cited 109× · PMID 28832957 · DOI 10.1111/bjh.14870
  4. BTK inhibitors in the treatment of hematological malignancies and inflammatory diseases: mechanisms and clinical studies.
    Alu A, Lei H, Han X, Wei Y, et al · · 2022 · cited 88× · PMID 36183125 · DOI 10.1186/s13045-022-01353-w
  5. Bruton's tyrosine kinase: from X-linked agammaglobulinemia toward targeted therapy for B-cell malignancies.
    Ponader S, Burger JA. · · 2014 · cited 86× · PMID 24778403 · DOI 10.1200/jco.2013.53.1046
  6. Ibrutinib versus temsirolimus: 3-year follow-up of patients with previously treated mantle cell lymphoma from the phase 3, international, randomized, open-label RAY study.
    Rule S, Jurczak W, Jerkeman M, Rusconi C, et al · · 2018 · cited 72× · PMID 29572505 · DOI 10.1038/s41375-018-0023-2
  7. Bruton Tyrosine Kinase Inhibitors in B-Cell Malignancies: Their Use and Differential Features.
    Shirley M. · · 2022 · cited 64× · PMID 34905129 · DOI 10.1007/s11523-021-00857-8
  8. Treatment Outcomes and Roles of Transplantation and Maintenance Rituximab in Patients With Previously Untreated Mantle Cell Lymphoma: Results From Large Real-World Cohorts.
    Martin P, Cohen JB, Wang M, Kumar A, et al · · 2023 · cited 54× · PMID 35763708 · DOI 10.1200/jco.21.02698

Verify or expand the search:

Other trials of Bendamustine

Trials testing the same drug.

Other recruiting trials for Mantle Cell Lymphoma

Currently open trials in the same condition.

Other Janssen Research & Development, LLC trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT01776840.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing