CFTR gene — Drug Target

All drugs that target CFTR gene — marketed and clinical-stage. Includes 1 drug classes acting on this target.

Drug classes

Gene therapy

Phase 2 pipeline (2)

• CBLB612 · BioLab 612 LLC · Gene therapy · Respiratory
  CBLB612 is a gene therapy that aims to treat certain conditions by delivering a healthy copy of the CFTR gene to cells.
• 4D-710 · 4D Molecular Therapeutics · Gene therapy · Cystic Fibrosis
  4D-710 is a gene therapy that uses an adeno-associated virus to deliver a functional copy of the CFTR gene to the lungs, correcting the underlying genetic defect in cystic fibrosis.