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CBLB612

BioLab 612 LLC · Phase 2 active Small molecule

CBLB612 is a gene therapy that aims to treat certain conditions by delivering a healthy copy of the CFTR gene to cells.

CBLB612 is a gene therapy that aims to treat certain conditions by delivering a healthy copy of the CFTR gene to cells. Used for Cystic fibrosis.

At a glance

Generic nameCBLB612
SponsorBioLab 612 LLC
Drug classGene therapy
TargetCFTR gene
ModalitySmall molecule
Therapeutic areaRespiratory
PhasePhase 2

Mechanism of action

CBLB612 uses a viral vector to deliver the CFTR gene to the lungs, where it can help restore normal function to the airway epithelial cells. This can potentially treat cystic fibrosis by improving lung function and reducing the risk of pulmonary exacerbations.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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