siRNA Therapeutics — Pipeline, Approvals, Sponsors

Small interfering RNA therapeutics — most clinically deployed via GalNAc conjugation for hepatocyte targeting. Onpattro / Givlaari / Leqvio / Amvuttra. Strong cardiometabolic + rare disease pipeline.

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Marketed
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Filed
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Phase 3
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Phase 2
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Phase 1
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Total

Marketed leaders

No marketed leaders tracked.

Recent approvals (last 30 days)

No approvals in the last 30 days.

Upcoming PDUFA (next 180 days)

No upcoming PDUFA in next 180 days.

Top sponsors in this modality

No sponsor data.

Drug classes within siRNA Therapeutics

No class breakdown.

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Other modalities

BiologicsMonoclonal AntibodiesSmall MoleculesAntibody-Drug ConjugatesCell TherapiesGene TherapiesGene EditingmRNA TherapeuticsAntisense OligonucleotidesBispecific AntibodiesVaccines

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing