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Vitamin C (Ascorbic Acid)

M.D. Anderson Cancer Center · FDA-approved active Small molecule

Vitamin C acts as an antioxidant and cofactor for enzymatic reactions, and at high doses may generate reactive oxygen species to selectively target cancer cells.

Vitamin C acts as an antioxidant and cofactor for enzymatic reactions, and at high doses may generate reactive oxygen species to selectively target cancer cells. Used for Adjunctive therapy in cancer treatment (investigational), General nutritional supplementation.

At a glance

Generic nameVitamin C (Ascorbic Acid)
Also known asVitamin C group
SponsorM.D. Anderson Cancer Center
Drug classAntioxidant / Micronutrient
ModalitySmall molecule
Therapeutic areaOncology
PhaseFDA-approved

Mechanism of action

Vitamin C (ascorbic acid) functions as a reducing agent and electron donor in multiple metabolic pathways, supporting collagen synthesis, immune function, and antioxidant defense. At pharmacological concentrations achieved through intravenous administration, it may generate hydrogen peroxide that preferentially damages cancer cells while sparing normal tissues, and may enhance chemotherapy efficacy or modulate tumor microenvironment.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results