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Sapropterin Dihydrochloride and Vitamin C
Sapropterin Dihydrochloride and Vitamin C is a Small molecule drug developed by BioMarin Pharmaceutical. It is currently in Phase 2 development. Also known as: 6R-BH4 and Vitamin C.
At a glance
| Generic name | Sapropterin Dihydrochloride and Vitamin C |
|---|---|
| Also known as | 6R-BH4 and Vitamin C |
| Sponsor | BioMarin Pharmaceutical |
| Modality | Small molecule |
| Phase | Phase 2 |
Approved indications
Common side effects
Key clinical trials
- Exercise and NO in HFrEF (EARLY_PHASE1)
- A Phase 2, Pharmacokinetic (PK) Study of 6R-BH4 Alone or 6R-BH4 With Vitamin C in Subjects With Endothelial Dysfunction (PHASE2)
- Long Term Nitric Oxide Bioavailability on Vascular Health in Chronic Obstructive Pulmonary Disease (PHASE2)
- Cystic Fibrosis and Endothelial Function: At Rest and During Exercise (PHASE2)
- Nitric Oxide Bioavailability in Chronic Obstructive Pulmonary Disease (COPD) (NA)
- Tetrahydrobiopterin in Patients With Chronic Kidney Disease (CKD) and Albuminuria (PHASE2)
Primary sources
Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.
| Source | Used for |
|---|---|
| ClinicalTrials.gov | Trial enrolment, design, endpoints, results |
Competitive intelligence
For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:
- Sapropterin Dihydrochloride and Vitamin C CI brief — competitive landscape report
- Sapropterin Dihydrochloride and Vitamin C updates RSS · CI watch RSS
- BioMarin Pharmaceutical portfolio CI
Frequently asked questions about Sapropterin Dihydrochloride and Vitamin C
What is Sapropterin Dihydrochloride and Vitamin C?
Sapropterin Dihydrochloride and Vitamin C is a Small molecule drug developed by BioMarin Pharmaceutical.
Who makes Sapropterin Dihydrochloride and Vitamin C?
Sapropterin Dihydrochloride and Vitamin C is developed by BioMarin Pharmaceutical (see full BioMarin Pharmaceutical pipeline at /company/biomarin-pharmaceutical).
Is Sapropterin Dihydrochloride and Vitamin C also known as anything else?
Sapropterin Dihydrochloride and Vitamin C is also known as 6R-BH4 and Vitamin C.
What development phase is Sapropterin Dihydrochloride and Vitamin C in?
Sapropterin Dihydrochloride and Vitamin C is in Phase 2.
Related
- Manufacturer: BioMarin Pharmaceutical — full pipeline
- Also known as: 6R-BH4 and Vitamin C
- Compare: Sapropterin Dihydrochloride and Vitamin C vs similar drugs
- Pricing: Sapropterin Dihydrochloride and Vitamin C cost, discount & access