Last reviewed · How we verify
rAAVrh74.MHCK7.DYSF.DV
At a glance
| Generic name | rAAVrh74.MHCK7.DYSF.DV |
|---|---|
| Sponsor | Sarepta Therapeutics, Inc. |
| Modality | Small molecule |
| Phase | Phase 1 |
Approved indications
Common side effects
Key clinical trials
- A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related) (PHASE1)
- rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies (PHASE1)
Primary sources
Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.
| Source | Used for |
|---|---|
| ClinicalTrials.gov | Trial enrolment, design, endpoints, results |
Competitive intelligence
For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:
- rAAVrh74.MHCK7.DYSF.DV CI brief — competitive landscape report
- rAAVrh74.MHCK7.DYSF.DV updates RSS · CI watch RSS
- Sarepta Therapeutics, Inc. portfolio CI