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Sarepta Therapeutics, Inc. — Portfolio Competitive Intelligence Brief
0 marketed
0 filed
3 Phase 3
0 Phase 2
3 Phase 1
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Portfolio leaders (marketed + Phase 3 / filed)
| Drug | Generic | Phase | Class | Target | Area | First approval |
|---|---|---|---|---|---|---|
| SRP-4053 | SRP-4053 | phase 3 | Antisense oligonucleotide | Dystrophin pre-mRNA (exon 53) | Neuromuscular/Genetic | |
| SRP-9003 | SRP-9003 | phase 3 | Antisense oligonucleotide | DMPK mRNA | Neuromuscular/Genetic Disorders | |
| SRP-4045 | SRP-4045 | phase 3 | Gene therapy | Dystrophin gene | Muscular dystrophy |
Therapeutic area mix
- Muscular dystrophy · 1
- Neuromuscular/Genetic · 1
- Neuromuscular/Genetic Disorders · 1
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Patent timeline (forward window)
Competitive overlap (companies sharing drug classes)
- Abeona Therapeutics, Inc · 1 shared drug class
- AskBio Inc · 1 shared drug class
- Avidity Biosciences, Inc. · 1 shared drug class
- BioLab 612 LLC · 1 shared drug class
- Brain Neurotherapy Bio, Inc. · 1 shared drug class
- Emily de los Reyes · 1 shared drug class
- European Organisation for Research and Treatment of Cancer - EORTC · 1 shared drug class
- 4D Molecular Therapeutics · 1 shared drug class
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Cite this brief
Drug Landscape (2026). Sarepta Therapeutics, Inc. — Portfolio Competitive Intelligence Brief. https://druglandscape.com/ci/company/sarepta-therapeutics-inc. Accessed 2026-05-16.