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oral isotretinoin
oral isotretinoin is a Retinoid Small molecule drug developed by Federal University of São Paulo. It is currently FDA-approved for Severe recalcitrant nodular acne, Acne at high risk of permanent scarring. Also known as: oral retinoid, roaccutane, Acnova, low-dose oral isotretinoin.
Isotretinoin is a potent retinoid that binds to nuclear retinoid receptors to regulate gene expression, reducing sebum production and normalizing epithelial cell differentiation in the skin.
Isotretinoin is a potent retinoid that binds to nuclear retinoid receptors to regulate gene expression, reducing sebum production and normalizing epithelial cell differentiation in the skin. Used for Severe recalcitrant nodular acne, Acne at high risk of permanent scarring.
At a glance
| Generic name | oral isotretinoin |
|---|---|
| Also known as | oral retinoid, roaccutane, Acnova, low-dose oral isotretinoin, off label use of oral isotretinoin |
| Sponsor | Federal University of São Paulo |
| Drug class | Retinoid |
| Target | Retinoid acid receptors (RAR), Retinoid X receptors (RXR) |
| Modality | Small molecule |
| Therapeutic area | Dermatology |
| Phase | FDA-approved |
Mechanism of action
Isotretinoin is a synthetic derivative of vitamin A that acts as a ligand for retinoid acid receptors (RAR) and retinoid X receptors (RXR) in the nucleus, modulating transcription of genes involved in sebaceous gland function, keratinocyte differentiation, and inflammation. It dramatically reduces sebaceous gland size and sebum production, and has anti-inflammatory and anti-proliferative effects on skin cells. These combined effects make it highly effective for severe acne by addressing multiple pathogenic factors.
Approved indications
- Severe recalcitrant nodular acne
- Acne at high risk of permanent scarring
Common side effects
- Cheilitis (lip inflammation)
- Dry skin and mucous membranes
- Elevated triglycerides
- Elevated liver enzymes
- Headache
- Photosensitivity
- Teratogenicity (if exposed during pregnancy)
Key clinical trials
- Metronomic Chemotherapy in Wilms Tumor (MetroWilms-1906) (PHASE1, PHASE2)
- Isotretinoin vs hCG for Male Infertility Due to Low or Absent Sperm (PHASE2)
- Testing the Addition of 131I-MIBG or Lorlatinib to Intensive Therapy in People With High-Risk Neuroblastoma (NBL) (PHASE3)
- Pilot Study of IT Topotecan and Maintenance Chemotherapy for HR-EBTs in Children < 6 Years, Post Consolidation (EARLY_PHASE1)
- Comparison of Combination of Itraconazole and Isotretinoin Versus Itraconazole Alone in the Treatment of Resistant Trichophyton Infection (NA)
- Induction Therapy Including 131 I-MIBG and Chemotherapy in Treating Patients With Newly Diagnosed High-Risk Neuroblastoma Undergoing Stem Cell Transplant, Radiation Therapy, and Maintenance Therapy With Isotretinoin (PHASE1)
- Efficacy of Cosmetic Product RV3278B-OS0386 in the Maintenance Phase After Oral Isotretinoin Treatment of Adults Subjects With Facial Acne. (NA)
- Effects of Isotretinoin on Smell (NA)
Primary sources
Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.
| Source | Used for |
|---|---|
| ClinicalTrials.gov | Trial enrolment, design, endpoints, results |
Competitive intelligence
For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:
- oral isotretinoin CI brief — competitive landscape report
- oral isotretinoin updates RSS · CI watch RSS
- Federal University of São Paulo portfolio CI
Frequently asked questions about oral isotretinoin
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Related
- Drug class: All Retinoid drugs
- Target: All drugs targeting Retinoid acid receptors (RAR), Retinoid X receptors (RXR)
- Manufacturer: Federal University of São Paulo — full pipeline
- Therapeutic area: All drugs in Dermatology
- Indication: Drugs for Severe recalcitrant nodular acne
- Indication: Drugs for Acne at high risk of permanent scarring
- Also known as: oral retinoid, roaccutane, Acnova, low-dose oral isotretinoin, off label use of oral isotretinoin
- Compare: oral isotretinoin vs similar drugs
- Pricing: oral isotretinoin cost, discount & access