EMA — authorised 19 November 2015
- Application: EMEA/H/C/003954
- Marketing authorisation holder: Vertex Pharmaceuticals (Ireland) Limited
- Local brand name: Orkambi
- Indication: Orkambi tablets are indicated for the treatment of cystic fibrosis (CF) in patients aged 6 years and older who are homozygous for the F508del mutation in the CFTR gene. Orkambi granules are indicated for the treatment of cystic fibrosis (CF) in children aged 1 year and older who are homozygous for the F508del mutation in the CFTR gene.
- Status: approved