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cyclo phosphamide

Al-Azhar University · FDA-approved active Small molecule

Cyclophosphamide is an alkylating agent that cross-links DNA strands, preventing cell division and causing cancer cell death.

Cyclophosphamide, an alkylating agent, is used in various hematological malignancies and autoimmune disorders. It is being evaluated in multiple clinical trials, including CAR T-cell therapy and stem cell transplantation. Despite no FDA label, it has off-label uses in lupus nephritis and multiple sclerosis.

At a glance

Generic namecyclo phosphamide
SponsorAl-Azhar University
Drug classAlkylating agent
TargetDNA
ModalitySmall molecule
Therapeutic areaOncology, Immunology
PhaseFDA-approved

Mechanism of action

Cyclophosphamide is a nitrogen mustard derivative that requires hepatic activation to form active metabolites. These metabolites covalently bind to DNA, creating inter- and intra-strand cross-links that inhibit DNA replication and transcription, leading to apoptosis. It is also immunosuppressive, depleting lymphocytes and suppressing antibody production.

Approved indications

Common side effects

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