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Cannabidiol Oral Solution [Epidiolex]

Silkiss Eye Surgery · FDA-approved active Small molecule

Cannabidiol modulates endocannabinoid signaling and multiple ion channels to reduce neuronal hyperexcitability and seizure activity.

Cannabidiol modulates endocannabinoid signaling and multiple ion channels to reduce neuronal hyperexcitability and seizure activity. Used for Dravet syndrome (severe myoclonic epilepsy of infancy), Lennox-Gastaut syndrome, Tuberous sclerosis complex-associated seizures.

At a glance

Generic nameCannabidiol Oral Solution [Epidiolex]
Also known asEpidiolex
SponsorSilkiss Eye Surgery
Drug classCannabinoid anticonvulsant
TargetTRP channels, adenosine signaling, serotonin receptors (multi-target)
ModalitySmall molecule
Therapeutic areaNeurology
PhaseFDA-approved

Mechanism of action

Cannabidiol (CBD) is a non-intoxicating cannabinoid that acts through multiple mechanisms including modulation of transient receptor potential (TRP) channels, enhancement of adenosine signaling, and effects on serotonin receptors. It reduces seizure frequency and severity in epilepsy by decreasing neuronal excitability without direct GABA receptor agonism. The exact molecular mechanisms remain incompletely understood but involve both cannabinoid receptor-independent and receptor-dependent pathways.

Approved indications

Common side effects

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