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Béfizal

Hôpital Necker-Enfants Malades · Phase 2 active Small molecule Under review

Béfizal is a SGLT2 inhibitor Small molecule drug developed by Hôpital Necker-Enfants Malades. It is currently in Phase 2 development for Type 2 diabetes.

Béfizal is a small molecule that targets the SGLT2 receptor.

Béfizal is a medication being studied for the treatment of Leber Hereditary Optic Neuropathy. It is being investigated in a clinical trial (NCT04561466) to assess its safety and efficacy in this condition.

Likelihood of approval
15.3% vs 15.3% industry baseline
If approved by FDA: likely 2031–2034
Steps remaining: Phase 3 → NDA/BLA submission
Confidence: Medium
Why this estimate
  • Baseline phase 2 → approval rate +15.3pp
    Industry-wide phase 2 drugs reach approval ~15.3% of the time (BIO/Informa 2023 industry benchmark across all therapeutic areas).
Predicted approval windows by jurisdiction (conditional on FDA approval)
Regulator Country Likely year Lag vs FDA
FDA US 2031–2034
EMA EU 2032–2035 +0.7 yr
MHRA GB 2032–2035 +0.7 yr
Health Canada CA 2032–2036 +0.9 yr
TGA AU 2032–2036 +1.2 yr
PMDA JP 2032–2036 +1.5 yr
NMPA CN 2033–2037 +2.3 yr
MFDS KR 2032–2036 +1.4 yr
CDSCO IN 2032–2037 +1.8 yr
ANVISA BR 2033–2037 +2.3 yr

Hover any row for the lag rationale. Lag estimates are reduced when the drug has FDA Breakthrough or EMA PRIME designation (sponsors file globally in parallel).

Estimate based on the BIO/Informa industry phase transition rates plus per-drug modifiers for therapeutic area, sponsor type, FDA designations, mechanism, and trial design. Per-jurisdiction lags from Tufts CSDD international approval studies. Not investment, clinical or regulatory advice. Methodology: /methodology#likelihood.

At a glance

Generic nameBéfizal
SponsorHôpital Necker-Enfants Malades
Drug classSGLT2 inhibitor
TargetSGLT2
ModalitySmall molecule
Therapeutic areaDiabetes
PhasePhase 2

Mechanism of action

By inhibiting SGLT2, Béfizal reduces glucose reabsorption in the kidneys, leading to decreased blood glucose levels. This mechanism is particularly useful in the treatment of type 2 diabetes.

Approved indications

Common side effects

Key clinical trials

Primary sources

Every claim on this page is sourced from regulatory or scientific primary sources. See our editorial policy for full methodology.

SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

Competitive intelligence

For the full competitive landscape — auto-detected comparators, recent regulatory actions across the set, upcoming PDUFA, patent timeline, sponsor landscape:

Frequently asked questions about Béfizal

What is Béfizal?

Béfizal is a SGLT2 inhibitor drug developed by Hôpital Necker-Enfants Malades, indicated for Type 2 diabetes.

How does Béfizal work?

Béfizal is a small molecule that targets the SGLT2 receptor.

What is Béfizal used for?

Béfizal is indicated for Type 2 diabetes.

Who makes Béfizal?

Béfizal is developed by Hôpital Necker-Enfants Malades (see full Hôpital Necker-Enfants Malades pipeline at /company/h-pital-necker-enfants-malades).

What drug class is Béfizal in?

Béfizal belongs to the SGLT2 inhibitor class. See all SGLT2 inhibitor drugs at /class/sglt2-inhibitor.

What development phase is Béfizal in?

Béfizal is in Phase 2.

What are the side effects of Béfizal?

Common side effects of Béfizal include Increased risk of genital yeast infections.

What does Béfizal target?

Béfizal targets SGLT2 and is a SGLT2 inhibitor.

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing