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AIR DNase

Protalix · Phase 2 active Small molecule

AIR DNase is a recombinant human deoxyribonuclease that degrades extracellular DNA to reduce mucus viscosity and improve airway clearance in cystic fibrosis.

AIR DNase is a recombinant human deoxyribonuclease that degrades extracellular DNA to reduce mucus viscosity and improve airway clearance in cystic fibrosis. Used for Cystic fibrosis.

At a glance

Generic nameAIR DNase
SponsorProtalix
Drug classRecombinant enzyme
TargetExtracellular DNA
ModalitySmall molecule
Therapeutic areaRespiratory / Pulmonary
PhasePhase 2

Mechanism of action

The drug breaks down DNA present in sputum and mucus secretions, which contributes to the thick, sticky consistency that obstructs airways in cystic fibrosis patients. By enzymatically degrading this extracellular DNA, AIR DNase reduces mucus viscosity and improves mucociliary clearance, potentially enhancing lung function and reducing respiratory infections.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results