PRX-102 (pegunigalsidase alfa) · Rare genetic disease / Lysosomal storage disorder PRX-102 is a pegylated recombinant human α-galactosidase A enzyme that breaks down accumulated globotriaosylceramide (Gb3) in cells affected by Fabry disease.
Phase 2 pipeline
AIR DNase · Respiratory / Pulmonary AIR DNase is a recombinant human deoxyribonuclease that degrades extracellular DNA to reduce mucus viscosity and improve airway clearance in cystic fibrosis.