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5-fluorouracil/oxaliplatin

Seoul National University Hospital · Phase 3 active Small molecule

5-fluorouracil/oxaliplatin is a Chemotherapy combination (antimetabolite + platinum agent) Small molecule drug developed by Seoul National University Hospital. It is currently in Phase 3 development for Colorectal cancer (metastatic and adjuvant settings), Gastric cancer, Pancreatic cancer.

5-fluorouracil inhibits thymidylate synthase to disrupt DNA synthesis, while oxaliplatin forms DNA cross-links, together providing synergistic cytotoxic effects against cancer cells.

5-fluorouracil inhibits thymidylate synthase to disrupt DNA synthesis, while oxaliplatin forms DNA cross-links, together providing synergistic cytotoxic effects against cancer cells. Used for Colorectal cancer (metastatic and adjuvant settings), Gastric cancer, Pancreatic cancer.

At a glance

Generic name5-fluorouracil/oxaliplatin
SponsorSeoul National University Hospital
Drug classChemotherapy combination (antimetabolite + platinum agent)
TargetThymidylate synthase (5-FU); DNA (oxaliplatin)
ModalitySmall molecule
Therapeutic areaOncology
PhasePhase 3

Mechanism of action

5-fluorouracil (5-FU) is a pyrimidine antimetabolite that blocks thymidylate synthase, preventing dTMP synthesis and disrupting DNA replication. Oxaliplatin is a third-generation platinum compound that forms interstrand and intrastrand DNA cross-links, leading to apoptosis. The combination (often called FOLFOX when combined with leucovorin and fluorouracil) exploits complementary mechanisms to enhance cytotoxicity against rapidly dividing cancer cells.

Approved indications

Common side effects

Key clinical trials

Primary sources

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SourceUsed for
ClinicalTrials.govTrial enrolment, design, endpoints, results

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Frequently asked questions about 5-fluorouracil/oxaliplatin

What is 5-fluorouracil/oxaliplatin?

5-fluorouracil/oxaliplatin is a Chemotherapy combination (antimetabolite + platinum agent) drug developed by Seoul National University Hospital, indicated for Colorectal cancer (metastatic and adjuvant settings), Gastric cancer, Pancreatic cancer.

How does 5-fluorouracil/oxaliplatin work?

5-fluorouracil inhibits thymidylate synthase to disrupt DNA synthesis, while oxaliplatin forms DNA cross-links, together providing synergistic cytotoxic effects against cancer cells.

What is 5-fluorouracil/oxaliplatin used for?

5-fluorouracil/oxaliplatin is indicated for Colorectal cancer (metastatic and adjuvant settings), Gastric cancer, Pancreatic cancer, Ovarian cancer.

Who makes 5-fluorouracil/oxaliplatin?

5-fluorouracil/oxaliplatin is developed by Seoul National University Hospital (see full Seoul National University Hospital pipeline at /company/seoul-national-university-hospital).

What drug class is 5-fluorouracil/oxaliplatin in?

5-fluorouracil/oxaliplatin belongs to the Chemotherapy combination (antimetabolite + platinum agent) class. See all Chemotherapy combination (antimetabolite + platinum agent) drugs at /class/chemotherapy-combination-antimetabolite-platinum-agent.

What development phase is 5-fluorouracil/oxaliplatin in?

5-fluorouracil/oxaliplatin is in Phase 3.

What are the side effects of 5-fluorouracil/oxaliplatin?

Common side effects of 5-fluorouracil/oxaliplatin include Neutropenia, Anemia, Thrombocytopenia, Nausea and vomiting, Diarrhea, Peripheral neuropathy.

What does 5-fluorouracil/oxaliplatin target?

5-fluorouracil/oxaliplatin targets Thymidylate synthase (5-FU); DNA (oxaliplatin) and is a Chemotherapy combination (antimetabolite + platinum agent).

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