Last reviewed · How we verify
Cholestanol storage disease
Approved treatments
- Cholbam · Mirum
Cholbam works by binding to the G-protein coupled bile acid receptor 1, which helps regulate bile acid levels in the body. - Cholbam · Mirum Pharmaceuticals, Inc.
Competitive intelligence
For the full treatment-landscape CI brief — marketed leaders side-by-side, pipeline by phase, recent regulatory actions, sponsor landscape:
- Cholestanol storage disease patent landscape — cliff calendar, originator estates, attackable patents
- Cholestanol storage disease treatment landscape brief
- Cholestanol storage disease treatment updates RSS
Frequently asked questions about Cholestanol storage disease
What drugs treat Cholestanol storage disease?
Tracked treatments include Cholbam.
What is the treatment for Cholestanol storage disease?
Standard treatment for Cholestanol storage disease includes Cholbam. See the treatment landscape page for first-line, second-line and salvage options.
Related
- Treatment landscape: Cholestanol storage disease patent cliff · Cholestanol storage disease CI report
- Treatment: Cholbam · Mirum
- Treatment: Cholbam · Mirum Pharmaceuticals, Inc.
- All diseases: Browse the disease index · Disease landscape hub
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing