{"disease":{"id":"cholestanol-storage-disease","name":"Cholestanol storage disease","therapeutic_area":"","data":{},"enrichment_level":0,"last_enriched_at":null,"visit_count":0,"created_at":"2026-04-19T18:31:21.150Z","updated_at":"2026-04-19T18:39:44.960Z","meddra_pt":null,"meddra_code":null,"icd10_codes":null,"synonyms":[],"prevalence_global":null,"prevalence_us":null,"marketed_drug_count":2,"pipeline_drug_count":0,"trial_count":0},"drugs":{"marketed":[{"drug_id":"cholic-acid","indication_name":"Cholestanol storage disease","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":"Cholbam","generic_name":"CHOLIC ACID","company_name":"Mirum","drug_phase":"marketed","molecular_target":"G-protein coupled bile acid receptor 1","drug_class":"Bile Acid [EPC]","quality_score":53,"revenue":null,"mechanism":"Cholbam works by binding to the G-protein coupled bile acid receptor 1, which helps regulate bile acid levels in the body."},{"drug_id":"cholbam","indication_name":"Cholestanol storage disease","indication_type":"approved","phase":null,"line_of_therapy":null,"is_primary_indication":false,"pivotal_trial_result":null,"pivotal_trial_p_value":null,"patient_population":null,"brand_name":null,"generic_name":"Cholbam","company_name":"Mirum Pharmaceuticals, Inc.","drug_phase":"marketed","molecular_target":"G-protein coupled bile acid receptor 1, Bile acid receptor","drug_class":"","quality_score":null,"revenue":null,"mechanism":null}],"pipeline":[],"offLabel":[],"totalMarketed":2,"totalPipeline":0},"trials":{"data":[],"total":0},"guidelines":[],"source":"Drug Landscape verified database"}