How many drugs treat Mucopolysaccharidosis, MPS-IV-A?

Drug Landscape tracks 1 marketed treatments for Mucopolysaccharidosis, MPS-IV-A (deduplicated by molecule). 0 Phase 3 candidates and 0 Phase 2 candidates are in the pipeline.

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Last reviewed 2026-06-10 · How we verify

Mucopolysaccharidosis, MPS-IV-A — Treatment Landscape & Competitive Intelligence

Name: Drug Landscape Pharmaceutical Database
Creator: Drug Landscape
Published: 2026-01-01
License: https://creativecommons.org/licenses/by/4.0/

Mucopolysaccharidosis, MPS-IV-A (disease) competitive landscape: 1 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

1 marketed 0 Phase 3 0 Phase 2 Live · 30-min refresh

Marketed treatment landscape

Approved drugs treating Mucopolysaccharidosis, MPS-IV-A, deduplicated by molecule. See the full disease page for line-of-therapy detail.

Drug	Generic	Sponsor	Class	Target	Line of therapy	First approval
Rhgalns	ELOSULFASE ALFA	BioMarin	Hydrolytic Lysosomal Glycosaminoglycan-specific Enzyme [EPC]	N-acetylgalactosamine-6-sulfatase		2014-01-01

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

BioMarin · 1 drug in Mucopolysaccharidosis, MPS-IV-A

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Every new regulatory action, PDUFA date, or trial completion in Mucopolysaccharidosis, MPS-IV-A:

Cite this brief

Drug Landscape (2026). Mucopolysaccharidosis, MPS-IV-A — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/mucopolysaccharidosis-mps-iv-a. Accessed 2026-06-10.

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing