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Last reviewed 2026-06-10 · How we verify

Late-infantile neuronal ceroid lipofuscinosis — Treatment Landscape & Competitive Intelligence

Name: Drug Landscape Pharmaceutical Database
Creator: Drug Landscape
Published: 2026-01-01
License: https://creativecommons.org/licenses/by/4.0/

Late-infantile neuronal ceroid lipofuscinosis (disease) competitive landscape: 1 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

1 marketed 0 Phase 3 0 Phase 2 Live · 30-min refresh

Marketed treatment landscape

Approved drugs treating Late-infantile neuronal ceroid lipofuscinosis, deduplicated by molecule. See the full disease page for line-of-therapy detail.

Drug	Generic	Sponsor	Class	Target	Line of therapy	First approval
Rhttp1	CERLIPONASE ALFA	BioMarin	Hydrolytic Lysosomal N-terminal Tripeptidyl Peptidase			2017-01-01

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

BioMarin · 1 drug in Late-infantile neuronal ceroid lipofuscinosis

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Every new regulatory action, PDUFA date, or trial completion in Late-infantile neuronal ceroid lipofuscinosis:

Cite this brief

Drug Landscape (2026). Late-infantile neuronal ceroid lipofuscinosis — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/late-infantile-neuronal-ceroid-lipofuscinosis. Accessed 2026-06-10.

Late-infantile neuronal ceroid lipofuscinosis full disease profile — treatment pathway, diagnostics, guidelines
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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing