How many drugs treat Hutchinson-Gilford syndrome?

Drug Landscape tracks 1 marketed treatments for Hutchinson-Gilford syndrome (deduplicated by molecule). 0 Phase 3 candidates and 0 Phase 2 candidates are in the pipeline.

How do I subscribe to ongoing alerts?

Subscribe to /feed/disease/hutchinson-gilford-syndrome.xml in Feedly / Inoreader. Every regulatory action, PDUFA date, or trial completion in this treatment area lands in your feed automatically.

Last reviewed 2026-06-10 · How we verify

Hutchinson-Gilford syndrome — Treatment Landscape & Competitive Intelligence

Name: Drug Landscape Pharmaceutical Database
Creator: Drug Landscape
Published: 2026-01-01
License: https://creativecommons.org/licenses/by/4.0/

Hutchinson-Gilford syndrome (disease) competitive landscape: 1 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

1 marketed 0 Phase 3 0 Phase 2 Live · 30-min refresh

Marketed treatment landscape

Approved drugs treating Hutchinson-Gilford syndrome, deduplicated by molecule. See the full disease page for line-of-therapy detail.

Drug	Generic	Sponsor	Class	Target	Line of therapy	First approval
Zokinvy	LONAFARNIB	Sentynl Theraps Inc	Farnesyltransferase Inhibitor [EPC]	farnesyltransferase		2020-01-01

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

Sentynl Theraps Inc · 1 drug in Hutchinson-Gilford syndrome

Subscribe to ongoing alerts

Every new regulatory action, PDUFA date, or trial completion in Hutchinson-Gilford syndrome:

Cite this brief

Drug Landscape (2026). Hutchinson-Gilford syndrome — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/hutchinson-gilford-syndrome. Accessed 2026-06-10.

Hutchinson-Gilford syndrome full disease profile — treatment pathway, diagnostics, guidelines
Browse all CI briefs
Build a custom feed

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing