How many drugs treat Hepatic porphyria?

Drug Landscape tracks 1 marketed treatments for Hepatic porphyria (deduplicated by molecule). 0 Phase 3 candidates and 0 Phase 2 candidates are in the pipeline.

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Subscribe to /feed/disease/hepatic-porphyria.xml in Feedly / Inoreader. Every regulatory action, PDUFA date, or trial completion in this treatment area lands in your feed automatically.

Last reviewed 2026-06-10 · How we verify

Hepatic porphyria — Treatment Landscape & Competitive Intelligence

Name: Drug Landscape Pharmaceutical Database
Creator: Drug Landscape
Published: 2026-01-01
License: https://creativecommons.org/licenses/by/4.0/

Hepatic porphyria (disease) competitive landscape: 1 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

1 marketed 0 Phase 3 0 Phase 2 Live · 30-min refresh

Marketed treatment landscape

Approved drugs treating Hepatic porphyria, deduplicated by molecule. See the full disease page for line-of-therapy detail.

Drug	Generic	Sponsor	Class	Target	Line of therapy	First approval
Givlaari	GIVOSIRAN	Alnylam Pharmaceuticals	Aminolevulinate Synthase 1-directed RNA Interaction	aminolevulinate synthase1 (ALAS1) mRNA		2019-01-01

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

Alnylam Pharmaceuticals · 1 drug in Hepatic porphyria

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Every new regulatory action, PDUFA date, or trial completion in Hepatic porphyria:

Cite this brief

Drug Landscape (2026). Hepatic porphyria — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/hepatic-porphyria. Accessed 2026-06-10.

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing