Last reviewed 2026-06-10 · How we verify

Familial lipoprotein lipase deficiency — Treatment Landscape & Competitive Intelligence

Familial lipoprotein lipase deficiency (disease) competitive landscape: 1 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

Marketed treatment landscape

Approved drugs treating Familial lipoprotein lipase deficiency, deduplicated by molecule. See the full disease page for line-of-therapy detail.

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

1. uniQure biopharma B.V. · 1 drug in Familial lipoprotein lipase deficiency

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Every new regulatory action, PDUFA date, or trial completion in Familial lipoprotein lipase deficiency:

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Cite this brief

Drug Landscape (2026). Familial lipoprotein lipase deficiency — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/familial-lipoprotein-lipase-deficiency. Accessed 2026-06-10.

Related

• Familial lipoprotein lipase deficiency full disease profile — treatment pathway, diagnostics, guidelines
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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing